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Integrative chemogenomic analysis identifies small molecules that partially rescue ΔF508-CFTR for cystic fibrosis.
Hodos, Rachel A; Strub, Matthew D; Ramachandran, Shyam; Meleshkevitch, Ella A; Boudko, Dmitri Y; Bridges, Robert J; Dudley, Joel T; McCray, Paul B.
Afiliação
  • Hodos RA; Institute for Next Generation Healthcare, Mount Sinai School of Medicine, New York, NY, USA.
  • Strub MD; Courant Institute for Mathematical Sciences, New York University, New York, NY, USA.
  • Ramachandran S; Department of Pediatrics, University of Iowa, Carver College of Medicine, Iowa City, IA, USA.
  • Meleshkevitch EA; Interdisciplinary Graduate Program in Genetics, University of Iowa, Iowa City, IA, USA.
  • Boudko DY; Editas Medicine, Cambridge, MA, USA.
  • Bridges RJ; Department of Physiology and Biophysics, Rosalind Franklin University, North Chicago, IL, USA.
  • Dudley JT; Department of Physiology and Biophysics, Rosalind Franklin University, North Chicago, IL, USA.
  • McCray PB; Department of Physiology and Biophysics, Rosalind Franklin University, North Chicago, IL, USA.
CPT Pharmacometrics Syst Pharmacol ; 10(5): 500-510, 2021 05.
Article em En | MEDLINE | ID: mdl-33934548

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística Tipo de estudo: Prognostic_studies Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística Tipo de estudo: Prognostic_studies Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article