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Three-year results of phase I retinal gene therapy trial for CNGA3-mutated achromatopsia: results of a non randomised controlled trial.
Reichel, Felix Friedrich; Michalakis, Stylianos; Wilhelm, Barbara; Zobor, Ditta; Muehlfriedel, Regine; Kohl, Susanne; Weisschuh, Nicole; Sothilingam, Vithiyanjali; Kuehlewein, Laura; Kahle, Nadine; Seitz, Immanuel; Paquet-Durand, Francois; Tsang, Stephen H; Martus, Peter; Peters, Tobias; Seeliger, Mathias; Bartz-Schmidt, Karl Ulrich; Ueffing, Marius; Zrenner, Eberhard; Biel, Martin; Wissinger, Bernd; Fischer, Dominik.
Afiliação
  • Reichel FF; Department of Ophthalmology, University Eye Hospital Tübingen, Tübingen, Germany, Tübingen, Germany.
  • Michalakis S; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
  • Wilhelm B; Department of Ophthalmology, University Hospital, LMU Munich, Munich, Bayern, Germany.
  • Zobor D; Department of Ophthalmology, University Eye Hospital Tübingen, Tübingen, Germany, Tübingen, Germany.
  • Muehlfriedel R; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
  • Kohl S; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
  • Weisschuh N; Molecular Genetics Laboratory, Institute for Ophthalmic Research, University of Tübingen, Tubingen, Baden-Württemberg, Germany.
  • Sothilingam V; Molecular Genetics Laboratory, Institute for Ophthalmic Research, University of Tübingen, Tubingen, Baden-Württemberg, Germany.
  • Kuehlewein L; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
  • Kahle N; Department of Ophthalmology, University Eye Hospital Tübingen, Tübingen, Germany, Tübingen, Germany.
  • Seitz I; University of Tübingen, Tübingen, Germany.
  • Paquet-Durand F; Department of Ophthalmology, University Eye Hospital Tübingen, Tübingen, Germany, Tübingen, Germany.
  • Tsang SH; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
  • Martus P; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
  • Peters T; Columbia University, New York City, new York, USA.
  • Seeliger M; University of Tübingen, Tübingen, Germany.
  • Bartz-Schmidt KU; University of Tübingen, Tübingen, Germany.
  • Ueffing M; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
  • Zrenner E; Department of Ophthalmology, University Eye Hospital Tübingen, Tübingen, Germany, Tübingen, Germany.
  • Biel M; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
  • Wissinger B; Department of Ophthalmology, University Eye Hospital Tübingen, Tübingen, Germany, Tübingen, Germany.
  • Fischer D; Institute for Ophthalmic Research, University of Tübingen, Tübingen, Baden-Württemberg, Germany.
Br J Ophthalmol ; 106(11): 1567-1572, 2022 11.
Article em En | MEDLINE | ID: mdl-34006508

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Defeitos da Visão Cromática Tipo de estudo: Clinical_trials Limite: Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Defeitos da Visão Cromática Tipo de estudo: Clinical_trials Limite: Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article