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Epigenome editing of the CFTR-locus for treatment of cystic fibrosis.
Kabadi, Ami M; Machlin, Leah; Dalal, Nikita; Lee, Rhianna E; McDowell, Ian; Shah, Nirav N; Drowley, Lauren; Randell, Scott H; Reddy, Timothy E.
Afiliação
  • Kabadi AM; Element Genomics, a UCB Pharma company, Durham, NC, USA. Electronic address: ami.kabadi@gmail.com.
  • Machlin L; Element Genomics, a UCB Pharma company, Durham, NC, USA.
  • Dalal N; Element Genomics, a UCB Pharma company, Durham, NC, USA.
  • Lee RE; Marsico Lung Institute, The University of North Carolina at Chapel Hill, Chapel Hill, NC, USA; Department of Cell Biology and Physiology, The University of North Carolina at Chapel Hill, Chapel Hill, NC, USA.
  • McDowell I; Element Genomics, a UCB Pharma company, Durham, NC, USA.
  • Shah NN; Element Genomics, a UCB Pharma company, Durham, NC, USA.
  • Drowley L; UCB Biosciences, Durham, NC, USA.
  • Randell SH; Marsico Lung Institute, The University of North Carolina at Chapel Hill, Chapel Hill, NC, USA; Department of Cell Biology and Physiology, The University of North Carolina at Chapel Hill, Chapel Hill, NC, USA. Electronic address: scott_randell@med.unc.edu.
  • Reddy TE; Element Genomics, a UCB Pharma company, Durham, NC, USA; Department of Biostatistics and Bioinformatics, Duke University Medical School, Durham, NC, USA. Electronic address: tim.reddy@duke.edu.
J Cyst Fibros ; 21(1): 164-171, 2022 01.
Article em En | MEDLINE | ID: mdl-34049825

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Sistemas CRISPR-Cas / Edição de Genes / Proteína 9 Associada à CRISPR Limite: Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Sistemas CRISPR-Cas / Edição de Genes / Proteína 9 Associada à CRISPR Limite: Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article