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The AAV9 Variant Capsid AAV-F Mediates Widespread Transgene Expression in Nonhuman Primate Spinal Cord After Intrathecal Administration.
Beharry, Adam; Gong, Yi; Kim, James C; Hanlon, Killian S; Nammour, Josette; Hieber, Kate; Eichler, Florian; Cheng, Ming; Stemmer-Rachamimov, Anat; Stankovic, Konstantina M; Welling, Duane Bradley; Ng, Carrie; Maguire, Casey A.
Afiliação
  • Beharry A; Flagship Biosciences, Inc., Westminster, Colorado, USA.
  • Gong Y; Department of Neurology, Massachusetts General Hospital, Charlestown, Massachusetts, USA.
  • Kim JC; Department of Neurology, Massachusetts General Hospital, Charlestown, Massachusetts, USA.
  • Hanlon KS; Department of Neurology, Massachusetts General Hospital, Charlestown, Massachusetts, USA.
  • Nammour J; Harvard Medical School, Boston, Massachusetts, USA.
  • Hieber K; Department of Neurology, Massachusetts General Hospital, Charlestown, Massachusetts, USA.
  • Eichler F; Flagship Biosciences, Inc., Westminster, Colorado, USA.
  • Cheng M; Department of Neurology, Massachusetts General Hospital, Charlestown, Massachusetts, USA.
  • Stemmer-Rachamimov A; Harvard Medical School, Boston, Massachusetts, USA.
  • Stankovic KM; Department of Neurology, Massachusetts General Hospital, Charlestown, Massachusetts, USA.
  • Welling DB; Harvard Medical School, Boston, Massachusetts, USA.
  • Ng C; Harvard Medical School, Boston, Massachusetts, USA.
  • Maguire CA; Department of Pathology, Massachusetts General Hospital, Boston, Massachusetts, USA.
Hum Gene Ther ; 33(1-2): 61-75, 2022 01.
Article em En | MEDLINE | ID: mdl-34128391

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Capsídeo / Dependovirus Limite: Animals Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Capsídeo / Dependovirus Limite: Animals Idioma: En Ano de publicação: 2022 Tipo de documento: Article