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Digital endpoints for self-administered home-based functional assessment in pediatric Friedreich's ataxia.
Mueller, Arne; Paterson, Elaine; McIntosh, Avery; Praestgaard, Jens; Bylo, Mary; Hoefling, Holger; Wells, McKenzie; Lynch, David R; Rummey, Christian; Krishnan, Michelle L; Schultz, Meredith; Malanga, C J.
Afiliação
  • Mueller A; Translational Medicine, Novartis Institutes for BioMedical Research, Basel, Switzerland.
  • Paterson E; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • McIntosh A; Novartis Development, Cambridge, Massachusetts, USA.
  • Praestgaard J; Novartis Development, Cambridge, Massachusetts, USA.
  • Bylo M; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Hoefling H; NIBR Informatics, Novartis Institute of Biomedical Research, Basel, Switzerland.
  • Wells M; Division of Neurology, Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.
  • Lynch DR; Division of Neurology, Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.
  • Rummey C; Clinical Data Science GmbH, Basel, Switzerland.
  • Krishnan ML; Translational Medicine, Novartis Institutes for BioMedical Research, Basel, Switzerland.
  • Schultz M; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Malanga CJ; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
Ann Clin Transl Neurol ; 8(9): 1845-1856, 2021 09.
Article em En | MEDLINE | ID: mdl-34355532

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Índice de Gravidade de Doença / Atividades Cotidianas / Ataxia de Friedreich / Técnicas de Diagnóstico Neurológico Tipo de estudo: Observational_studies / Prevalence_studies / Risk_factors_studies Limite: Adolescent / Child / Female / Humans / Male Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Índice de Gravidade de Doença / Atividades Cotidianas / Ataxia de Friedreich / Técnicas de Diagnóstico Neurológico Tipo de estudo: Observational_studies / Prevalence_studies / Risk_factors_studies Limite: Adolescent / Child / Female / Humans / Male Idioma: En Ano de publicação: 2021 Tipo de documento: Article