Clinical development innovation in rare diseases: lessons learned and best practices from the DevelopAKUre consortium.

Rudebeck, Mattias; Scott, Ciarán; Rhodes, Nicholas P; van Kan, Christa; Olsson, Birgitta; Al-Sbou, Mohammed; Hall, Anthony K; Sireau, Nicolas; Ranganath, Lakshminarayan R

Rudebeck, Mattias; Scott, Ciarán; Rhodes, Nicholas P; van Kan, Christa; Olsson, Birgitta; Al-Sbou, Mohammed; Hall, Anthony K; Sireau, Nicolas; Ranganath, Lakshminarayan R.

Afiliação

Rudebeck M; Swedish Orphan Biovitrum (Sobi), Stockholm, Sweden.
Scott C; AKU Society, Cambridge, CB1 2BL, UK.
Rhodes NP; Liverpool University Hospitals NHS Foundation Trust, Liverpool, UK.
van Kan C; PSR Group, Hoofddorp, The Netherlands.
Olsson B; Swedish Orphan Biovitrum (Sobi), Stockholm, Sweden.
Al-Sbou M; Faculty of Medicine, Mutah University, Karak, Jordan.
Hall AK; Cudos, Hoofddorp, The Netherlands.
Sireau N; AKU Society, Cambridge, CB1 2BL, UK. nick@akusociety.org.
Ranganath LR; Liverpool University Hospitals NHS Foundation Trust, Liverpool, UK.

Orphanet J Rare Dis ; 16(1): 510, 2021 12 14.

Article em En | MEDLINE | ID: mdl-34906169

Assuntos

Doenças Raras; Humanos

Palavras-chave

AKU; Alkaptonuria; Best practice; DevelopAKUre; Drug development; Rare diseases

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Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doenças Raras Tipo de estudo: Guideline / Prognostic_studies Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

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