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Efficacy of Burosumab in Adults with X-linked Hypophosphatemia (XLH): A Post Hoc Subgroup Analysis of a Randomized Double-Blind Placebo-Controlled Phase 3 Study.
Brandi, Maria Luisa; Jan de Beur, Suzanne; Briot, Karine; Carpenter, Thomas; Cheong, Hae Il; Cohen-Solal, Martine; Crowley, Rachel K; Eastell, Richard; Imanishi, Yasuo; Imel, Erik A; Ing, Steven W; Insogna, Karl; Ito, Nobuaki; Javaid, Kassim; Kamenicky, Peter; Keen, Richard; Kubota, Takuo; Lachmann, Robin H; Perwad, Farzana; Pitukcheewanont, Pisit; Portale, Anthony; Ralston, Stuart H; Tanaka, Hiroyuki; Weber, Thomas J; Yoo, Han-Wook; Sun, Wei; Williams, Angela; Nixon, Annabel; Takeuchi, Yasuhiro.
Afiliação
  • Brandi ML; FIRMO Foundation, Via San Gallo 123, 50100, Florence, Italy. marialuisa@marialuisabrandi.it.
  • Jan de Beur S; Division of Endocrinology and Metabolism, Department of Medicine, Johns Hopkins University School of Medicine, Baltimore, MD, USA.
  • Briot K; Department of Rheumatology, Cochin Hospital, Paris University, Paris, France.
  • Carpenter T; Department of Pediatrics and Department of Orthopedics and Rehabilitation, Yale School of Medicine, New Haven, CT, USA.
  • Cheong HI; Department of Pediatrics, Seoul National University Children's Hospital, Seoul, Republic of Korea.
  • Cohen-Solal M; Department of Rheumatology, Lariboisière Hospital, INSERM U1132 BIOSCAR, and University of Paris, Paris, France.
  • Crowley RK; Department of Endocrinology, St Vincent's University Hospital, and University College Dublin School of Medicine and Medical Science, Dublin, Ireland.
  • Eastell R; Department of Oncology and Metabolism, University of Sheffield, Sheffield, UK.
  • Imanishi Y; Department of Metabolism, Endocrinology and Molecular Medicine, Osaka Metropolitan University Graduate School of Medicine, Osaka, Japan.
  • Imel EA; Department of Medicine and Department of Pediatrics, Indiana University School of Medicine, Indianapolis, IN, USA.
  • Ing SW; Division of Endocrinology, Diabetes, and Metabolism, Ohio State University Wexner Medical Center, Columbus, OH, USA.
  • Insogna K; Department of Internal Medicine, Yale School of Medicine, New Haven, CT, USA.
  • Ito N; Division of Nephrology and Endocrinology, The University of Tokyo Hospital, Tokyo, Japan.
  • Javaid K; Nuffield Department of Orthopaedics, Rheumatology and Musculoskeletal Sciences, National Institute for Health Research Oxford Biomedical Research Centre, University of Oxford, Oxford, UK.
  • Kamenicky P; Endocrine Physiology and Pathophysiology, INSERM, Paris-Saclay University, and Bicêtre Hospital, Paris, France.
  • Keen R; Metabolic Bone Disease Unit, Royal National Orthopaedic Hospital NHS Trust, London, UK.
  • Kubota T; Department of Pediatrics, Osaka University Graduate School of Medicine, Osaka, Japan.
  • Lachmann RH; Charles Dent Metabolic Unit, National Hospital for Neurology and Neurosurgery, University College London Hospitals NHS Foundation Trust, London, UK.
  • Perwad F; Division of Nephrology, Department of Pediatrics, University of California San Francisco, San Francisco, USA.
  • Pitukcheewanont P; Department of Pediatric Endocrinology, Children's Hospital Los Angeles, University of Southern California Keck School of Medicine, Los Angeles, USA.
  • Portale A; Division of Nephrology, Department of Pediatrics, University of California San Francisco, San Francisco, USA.
  • Ralston SH; Rheumatology and Bone Diseases Unit, Medical Research Council Institute of Genetics and Molecular Medicine, University of Edinburgh, Edinburgh, UK.
  • Tanaka H; Department of Pediatrics, Okayama Saiseikai General Hospital, Okayama, Japan.
  • Weber TJ; Division of Endocrinology, Metabolism and Nutrition, Department of Medicine, Duke University Medical Center, Durham, NC, USA.
  • Yoo HW; Department of Pediatrics, Asan Medical Center Children's Hospital, Seoul, Republic of Korea.
  • Sun W; Biostatistics Department, Kyowa Kirin Pharmaceutical Development, Inc., Princeton, NJ, USA.
  • Williams A; Kyowa Kirin International, Marlow, UK.
  • Nixon A; Chilli Consultancy, Salisbury, UK.
  • Takeuchi Y; Endocrine Center, Toranomon Hospital, Tokyo, Japan.
Calcif Tissue Int ; 111(4): 409-418, 2022 10.
Article em En | MEDLINE | ID: mdl-35927518

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Raquitismo Hipofosfatêmico Familiar Tipo de estudo: Clinical_trials Limite: Adult / Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Raquitismo Hipofosfatêmico Familiar Tipo de estudo: Clinical_trials Limite: Adult / Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article