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GENE TARGET: A framework for evaluating Mendelian neurodevelopmental disorders for gene therapy.
Chopra, Maya; Modi, Meera E; Dies, Kira A; Chamberlin, Nancy L; Buttermore, Elizabeth D; Brewster, Stephanie Jo; Prock, Lisa; Sahin, Mustafa.
Afiliação
  • Chopra M; Rosamund Stone Zander Translational Neuroscience Center, Department of Neurology, Boston Children's Hospital, Boston, MA 02115, USA.
  • Modi ME; Rosamund Stone Zander Translational Neuroscience Center, Department of Neurology, Boston Children's Hospital, Boston, MA 02115, USA.
  • Dies KA; Rosamund Stone Zander Translational Neuroscience Center, Department of Neurology, Boston Children's Hospital, Boston, MA 02115, USA.
  • Chamberlin NL; Rosamund Stone Zander Translational Neuroscience Center, Department of Neurology, Boston Children's Hospital, Boston, MA 02115, USA.
  • Buttermore ED; Rosamund Stone Zander Translational Neuroscience Center, Department of Neurology, Boston Children's Hospital, Boston, MA 02115, USA.
  • Brewster SJ; Rosamund Stone Zander Translational Neuroscience Center, Department of Neurology, Boston Children's Hospital, Boston, MA 02115, USA.
  • Prock L; Rosamund Stone Zander Translational Neuroscience Center, Department of Neurology, Boston Children's Hospital, Boston, MA 02115, USA.
  • Sahin M; Division of Developmental Medicine, Boston Children's Hospital, Boston, MA 02115, USA.
Mol Ther Methods Clin Dev ; 27: 32-46, 2022 Dec 08.
Article em En | MEDLINE | ID: mdl-36156879

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Ano de publicação: 2022 Tipo de documento: Article