Experience and Perspectives in the US on the Evolving Treatment Landscape in Spinal Muscular Atrophy.

Ramos-Platt, Leigh; Elman, Lauren; Shieh, Perry B

Ramos-Platt, Leigh; Elman, Lauren; Shieh, Perry B.

Afiliação

Ramos-Platt L; Department of Pediatrics, Keck School of Medicine, University of Southern California and Children's Hospital of Los Angeles, Los Angeles, CA, USA.
Elman L; Department of Neurology, University of Pennsylvania, Philadelphia, PA, USA.
Shieh PB; Department of Neurology and Pediatrics, University of California Los Angeles, Los Angeles, CA, USA.

Int J Gen Med ; 15: 7341-7353, 2022.

Article em En | MEDLINE | ID: mdl-36157294

Palavras-chave

nusinersen; onasemnogene abeparvovec-xioi; risdiplam; spinal muscular atrophy

Texto completo

Imprimir

XML

PubMed Links

Buscar no Google

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Prognostic_studies / Qualitative_research Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo

Imprimir

XML

PubMed Links

Buscar no Google