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Enhancing interaction of actin and actin-binding domain 1 of dystrophin with modulators: Toward improved gene therapy for Duchenne muscular dystrophy.
Guhathakurta, Piyali; Carter, Anna L; Thompson, Andrew R; Kurila, Dillon; LaFrence, Jeffrey; Zhang, Li; Trask, Jake R; Vanderheyden, Bri; Muretta, Joseph M; Ervasti, James M; Thomas, David D.
Afiliação
  • Guhathakurta P; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Carter AL; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Thompson AR; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Kurila D; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • LaFrence J; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Zhang L; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Trask JR; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Vanderheyden B; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Muretta JM; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Ervasti JM; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA.
  • Thomas DD; Department of Biochemistry, Molecular Biology and Biophysics, University of Minnesota, Minneapolis, Minnesota, USA. Electronic address: ddt@umn.edu.
J Biol Chem ; 298(12): 102675, 2022 12.
Article em En | MEDLINE | ID: mdl-36372234

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Distrofina / Actinas / Distrofia Muscular de Duchenne Limite: Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Distrofina / Actinas / Distrofia Muscular de Duchenne Limite: Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article