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Prenatal asfotase alfa-mediated enzyme replacement therapy restores delayed calcification in a severe infantile form of hypophosphatasia model mice.
Yoshida, Kaori; Ishizuka, Satoshi; Nakamura-Takahashi, Aki; Hasegawa, Akihiro; Umezawa, Akihiro; Koshika, Kyotaro; Ichinohe, Tatsuya; Kasahara, Masataka.
Afiliação
  • Yoshida K; Department of Dental Anesthesiology, Tokyo Dental College, Tokyo, Japan.
  • Ishizuka S; Department of Pharmacology, Tokyo Dental College, Tokyo, Japan.
  • Nakamura-Takahashi A; Department of Pharmacology, Tokyo Dental College, Tokyo, Japan. Electronic address: atakahashi@tdc.ac.jp.
  • Hasegawa A; Department of Obstetrics and Gynecology, The Jikei University School of Medicine, Tokyo, Japan; Center for Regenerative Medicine, National Center for Child Health and Development Research Institute, Tokyo, Japan.
  • Umezawa A; Center for Regenerative Medicine, National Center for Child Health and Development Research Institute, Tokyo, Japan.
  • Koshika K; Department of Dental Anesthesiology, Tokyo Dental College, Tokyo, Japan.
  • Ichinohe T; Department of Dental Anesthesiology, Tokyo Dental College, Tokyo, Japan.
  • Kasahara M; Department of Pharmacology, Tokyo Dental College, Tokyo, Japan.
Eur J Med Genet ; 66(7): 104787, 2023 Jul.
Article em En | MEDLINE | ID: mdl-37209904

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Calcinose / Hipofosfatasia Limite: Animals / Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Calcinose / Hipofosfatasia Limite: Animals / Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article