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Target Product Profile for Cutaneous Neurofibromas: Clinical Trials to Prevent, Arrest, or Regress Cutaneous Neurofibromas.
Ly, Ina; Romo, Carlos G; Gottesman, Sally; Kelly, Kristen M; Kornacki, Deanna; York, Zachary; Lee, Sang Y; Rhodes, Steven D; Staedtke, Verena; Steensma, Matthew R; Blakeley, Jaishri O; Wolkenstein, Pierre.
Afiliação
  • Ly I; Stephen E. and Catherine Pappas Center for Neuro-Oncology, Massachusetts General Hospital, Boston, Massachusetts, USA. Electronic address: ily@partners.org.
  • Romo CG; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
  • Gottesman S; Neurofibromatosis Therapeutic Acceleration Program (NTAP), Baltimore, Maryland, USA; Children's Tumor Foundation, New York, New York, USA.
  • Kelly KM; Department of Dermatology, School of Medicine, University of California, Irvine, Irvine, California, USA.
  • Kornacki D; Incyte Corporation, Wilmington, Delaware, USA.
  • York Z; Independent, Neurofibromatosis type 1 patient.
  • Lee SY; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
  • Rhodes SD; Division of Hematology/Oncology, Department of Pediatrics, Indiana University School of Medicine, Indianapolis, Indiana, USA.
  • Staedtke V; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
  • Steensma MR; Helen Devos Children's Hospital, Spectrum Health System, Grand Rapids, Michigan, USA.
  • Blakeley JO; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
  • Wolkenstein P; Department of Dermatology, Henri Mondor Hospital, University Paris East Créteil, Créteil, France.
J Invest Dermatol ; 143(8): 1388-1396, 2023 08.
Article em En | MEDLINE | ID: mdl-37294242

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Neoplasias Cutâneas / Neurofibromatose 1 / Neurofibroma Limite: Adult / Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Neoplasias Cutâneas / Neurofibromatose 1 / Neurofibroma Limite: Adult / Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article