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Targeting AAV vectors to the central nervous system by engineering capsid-receptor interactions that enable crossing of the blood-brain barrier.
Huang, Qin; Chen, Albert T; Chan, Ken Y; Sorensen, Hikari; Barry, Andrew J; Azari, Bahar; Zheng, Qingxia; Beddow, Thomas; Zhao, Binhui; Tobey, Isabelle G; Moncada-Reid, Cynthia; Eid, Fatma-Elzahraa; Walkey, Christopher J; Ljungberg, M Cecilia; Lagor, William R; Heaney, Jason D; Chan, Yujia A; Deverman, Benjamin E.
Afiliação
  • Huang Q; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Chen AT; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Chan KY; Biological and Biomedical Sciences, Harvard University, Cambridge, Massachusetts, United States of America.
  • Sorensen H; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Barry AJ; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Azari B; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Zheng Q; Electrical & Computer Engineering Department, Northeastern University, Boston, Massachusetts, United States of America.
  • Beddow T; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Zhao B; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Tobey IG; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Moncada-Reid C; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Eid FE; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Walkey CJ; Stanley Center for Psychiatric Research, Broad Institute of MIT and Harvard, Cambridge, Massachusetts, United States of America.
  • Ljungberg MC; Department of Systems and Computer Engineering, Al-Azhar University, Cairo, Egypt.
  • Lagor WR; Department of Integrative Physiology, Baylor College of Medicine, Houston, Texas, United States of America.
  • Heaney JD; Department of Pediatrics, Baylor College of Medicine, Houston, Texas, United States of America.
  • Chan YA; Duncan Neurological Research Institute at Texas Children's Hospital, Houston, Texas, United States of America.
  • Deverman BE; Department of Integrative Physiology, Baylor College of Medicine, Houston, Texas, United States of America.
PLoS Biol ; 21(7): e3002112, 2023 07.
Article em En | MEDLINE | ID: mdl-37467291

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Barreira Hematoencefálica / Capsídeo Limite: Animals Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Barreira Hematoencefálica / Capsídeo Limite: Animals Idioma: En Ano de publicação: 2023 Tipo de documento: Article