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Partial genome content within rAAVs impacts performance in a cell assay-dependent manner.
Troxell, Bryan; Jaslow, Sarah L; Tsai, I-Wei; Sullivan, Chelsea; Draper, Benjamin E; Jarrold, Martin F; Lindsey, Kate; Blue, Levi.
Afiliação
  • Troxell B; StrideBio Analytical Development and Quality Control, 5 Laboratory Drive, Suite 1200, Research Triangle Park, NC 27709, USA.
  • Jaslow SL; AjaxBio, LLC, Holly Springs, NC 27540, USA.
  • Tsai IW; StrideBio Analytical Development and Quality Control, 5 Laboratory Drive, Suite 1200, Research Triangle Park, NC 27709, USA.
  • Sullivan C; StrideBio Analytical Development and Quality Control, 5 Laboratory Drive, Suite 1200, Research Triangle Park, NC 27709, USA.
  • Draper BE; StrideBio Analytical Development and Quality Control, 5 Laboratory Drive, Suite 1200, Research Triangle Park, NC 27709, USA.
  • Jarrold MF; Megadalton Solutions, Inc., 3750 E. Bluebird Ln., Bloomington, IN 47401, USA.
  • Lindsey K; Chemistry Department, Indiana University, 800 E. Kirkwood Avenue, Bloomington, IN 47405, USA.
  • Blue L; StrideBio Analytical Development and Quality Control, 5 Laboratory Drive, Suite 1200, Research Triangle Park, NC 27709, USA.
Mol Ther Methods Clin Dev ; 30: 288-302, 2023 Sep 14.
Article em En | MEDLINE | ID: mdl-37583716

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Ano de publicação: 2023 Tipo de documento: Article