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Long-term effectiveness of eculizumab: Data from the International PNH Registry.
Terriou, Louis; Lee, Jong Wook; Forsyth, Cecily; Griffin, Morag; Szer, Jeff; Röth, Alexander; Gustovic, Philippe; Metzger, Jesse; Patel, Ami S; Patriquin, Christopher J.
Afiliação
  • Terriou L; Université de Lille, Inserm, CHU Lille, Service de Médecine Interne et Immunologie Clinique, Centre de Référence des Maladies Autoimmunes Systémiques Rares du Nord et Nord-Ouest de France (CeRAINO), Institut de Recherche Translationnelle sur l'Inflammation (INFINITE) - U1286, Lille, France.
  • Lee JW; Department of Hematology, Seoul St. Mary's Hospital, The Catholic University of Korea, Seoul, Republic of Korea.
  • Forsyth C; Central Coast Haematology, North Gosford, New South Wales, Australia.
  • Griffin M; Department of Haematology, Leeds Teaching Hospitals NHS Trust, Leeds, UK.
  • Szer J; Department of Clinical Haematology, Peter MacCallum Cancer Centre and the Royal Melbourne Hospital, Melbourne, Victoria, Australia.
  • Röth A; Department of Hematology and Stem Cell Transplantation, University Hospital Essen and University of Duisburg-Essen, Essen, Germany.
  • Gustovic P; Alexion, AstraZeneca Rare Disease, Zürich, Switzerland.
  • Metzger J; Parexel, Newton, Massachusetts, USA.
  • Patel AS; Alexion, AstraZeneca Rare Disease, Boston, Massachusetts, USA.
  • Patriquin CJ; Division of Hematology, University of Toronto, Toronto, Ontario, Canada.
Eur J Haematol ; 111(5): 796-804, 2023 Nov.
Article em En | MEDLINE | ID: mdl-37712908

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hemoglobinúria Paroxística Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Humans / Infant Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hemoglobinúria Paroxística Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Humans / Infant Idioma: En Ano de publicação: 2023 Tipo de documento: Article