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Efficacy of Adeno-Associated Virus Serotype 9-Mediated Gene Therapy for AB-Variant GM2 Gangliosidosis.
Vyas, Meera; Deschenes, Natalie M; Osmon, Karlaina J L; Chen, Zhilin; Ahmad, Imtiaz; Kot, Shalini; Thompson, Patrick; Richmond, Chris; Gray, Steven J; Walia, Jagdeep S.
Afiliação
  • Vyas M; Centre for Neuroscience Studies, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Deschenes NM; Centre for Neuroscience Studies, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Osmon KJL; Centre for Neuroscience Studies, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Chen Z; Department of Biomedical and Molecular Sciences, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Ahmad I; Centre for Neuroscience Studies, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Kot S; Department of Biomedical and Molecular Sciences, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Thompson P; Department of Pediatrics, Queen's University, Kingston, ON K7L 2V7, Canada.
  • Richmond C; Department of Biomedical and Molecular Sciences, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Gray SJ; Department of Pediatrics, UT Southwestern Medical Center, Dallas, TX 75390, USA.
  • Walia JS; Centre for Neuroscience Studies, Queen's University, Kingston, ON K7L 3N6, Canada.
Int J Mol Sci ; 24(19)2023 Sep 27.
Article em En | MEDLINE | ID: mdl-37834060

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Tay-Sachs / Gangliosidoses GM2 Limite: Animals / Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Tay-Sachs / Gangliosidoses GM2 Limite: Animals / Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article