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Ruxolitinib Rescues Multiorgan Clinical Autoimmunity in Patients with APS-1.
Lévy, Romain; Escudier, Agathe; Bastard, Paul; Briand, Coralie; Polivka, Laura; Stoupa, Athanasia; Talbotec, Cécile; Rothenbuhler, Anya; Charbit, Marina; Debray, Dominique; Bodemer, Christine; Casanova, Jean-Laurent; Linglart, Agnès; Neven, Bénédicte.
Afiliação
  • Lévy R; Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM, Necker Hospital for Sick Children, Paris, EU, France. romain.levy@inserm.fr.
  • Escudier A; Paris-Cité University, Imagine Institute, Paris, EU, France. romain.levy@inserm.fr.
  • Bastard P; Pediatric Hematology, Immunology and Rheumatology Unit, Necker Hospital for Sick Children, AP-HP, Paris, EU, France. romain.levy@inserm.fr.
  • Briand C; St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA. romain.levy@inserm.fr.
  • Polivka L; Paris-Cité University, Imagine Institute, Paris, EU, France.
  • Stoupa A; Pediatric Hematology, Immunology and Rheumatology Unit, Necker Hospital for Sick Children, AP-HP, Paris, EU, France.
  • Talbotec C; Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM, Necker Hospital for Sick Children, Paris, EU, France.
  • Rothenbuhler A; Paris-Cité University, Imagine Institute, Paris, EU, France.
  • Charbit M; Pediatric Hematology, Immunology and Rheumatology Unit, Necker Hospital for Sick Children, AP-HP, Paris, EU, France.
  • Debray D; St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.
  • Bodemer C; Department of Pediatrics, Jean Verdier Hospital, AP-HP, Bondy, EU, France.
  • Casanova JL; Paris-Cité University, Imagine Institute, Paris, EU, France.
  • Linglart A; Department of Dermatology, Reference Center for Genodermatoses (MAGEC), Imagine Institute, Necker Hospital for Sick Children, AP-HP, Paris, EU, France.
  • Neven B; Pediatric Endocrinology, Gynecology and Diabetology Department, Necker Hospital for Sick Children, AP-HP, Paris, EU, France.
J Clin Immunol ; 44(1): 5, 2023 12 19.
Article em En | MEDLINE | ID: mdl-38112858

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Candidíase / Poliendocrinopatias Autoimunes / Inibidores de Janus Quinases Limite: Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Candidíase / Poliendocrinopatias Autoimunes / Inibidores de Janus Quinases Limite: Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article