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Long-term quality of life after hematopoietic cell transplant for sickle cell disease in childhood: A STELLAR interim analysis.
Arnold, Staci D; Bakshi, Nitya; Ross, Diana; Smith, Crystal; Sinha, Cynthia; Veludhandi, Anirudh; Dutreuil, Valerie; Bai, Shasha; Meacham, Lillian R; Guilcher, Greg; Bhatia, Monica; Abraham, Allistair; Kasow, Kimberly A; Haight, Ann; El Rassi, Fuad; Stenger, Elizabeth; Lipscomb, Joseph; Krishnamurti, Lakshmanan.
Afiliação
  • Arnold SD; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Bakshi N; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Ross D; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Smith C; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Sinha C; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Veludhandi A; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Dutreuil V; Pediatric Biostatistics Core, Department of Pediatrics, Emory School of Medicine, Atlanta, Georgia, USA.
  • Bai S; Pediatric Biostatistics Core, Department of Pediatrics, Emory School of Medicine, Atlanta, Georgia, USA.
  • Meacham LR; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Guilcher G; Alberta Children's Hospital, Calgary, Alberta, Canada.
  • Bhatia M; Division of Pediatric Hematology, Oncology, and Stem Cell Transplantation, Columbia University Medical Center, New York, New York, USA.
  • Abraham A; Children's National Hospital, Washington, DC, USA.
  • Kasow KA; Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, Maryland, USA.
  • Haight A; Lineberger Comprehensive Cancer Center, University of North Carolina, Chapel Hill, North Carolina, USA.
  • El Rassi F; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Stenger E; Georgia Comprehensive Sickle Cell Center at Grady Health System, Emory University School of Medicine, Atlanta, Georgia, USA.
  • Lipscomb J; Department of Pediatrics, Aflac Cancer and Blood Disorders Center at Children's Healthcare of Atlanta, Emory University, Atlanta, Georgia, USA.
  • Krishnamurti L; Emory University Rollins School of Public Health, Atlanta, Georgia, USA.
Am J Hematol ; 2024 Aug 06.
Article em En | MEDLINE | ID: mdl-39105410
ABSTRACT
We prospectively collected PROMIS©25 and PROMIS©29 surveys in the Sickle Cell Transplant Evaluation of Long Term and Late Effects Registry (STELLAR). Mobility and social participation T-scores were decreased; all other domains were within the norm.

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Ano de publicação: 2024 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Ano de publicação: 2024 Tipo de documento: Article