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CRISPR-Cas9-based treatment of myocilin-associated glaucoma.
Jain, Ankur; Zode, Gulab; Kasetti, Ramesh B; Ran, Fei A; Yan, Winston; Sharma, Tasneem P; Bugge, Kevin; Searby, Charles C; Fingert, John H; Zhang, Feng; Clark, Abbot F; Sheffield, Val C.
Afiliação
  • Jain A; Department of Pediatrics, Carver College of Medicine, University of Iowa, Iowa City, IA 52242.
  • Zode G; North Texas Eye Research Institute, University of North Texas Health Science Center, Fort Worth, TX 76107; gulab.zode@unthsc.edu val-sheffield@uiowa.edu.
  • Kasetti RB; North Texas Eye Research Institute, University of North Texas Health Science Center, Fort Worth, TX 76107.
  • Ran FA; McGovern Institute for Brain Research, Massachusetts Institute of Technology, Cambridge, MA 02142.
  • Yan W; McGovern Institute for Brain Research, Massachusetts Institute of Technology, Cambridge, MA 02142.
  • Sharma TP; Stephen A. Wynn Institute for Vision Research, Department of Ophthalmology, Carver College of Medicine, University of Iowa, Iowa City, IA 52242.
  • Bugge K; Department of Pediatrics, Carver College of Medicine, University of Iowa, Iowa City, IA 52242.
  • Searby CC; Department of Pediatrics, Carver College of Medicine, University of Iowa, Iowa City, IA 52242.
  • Fingert JH; Stephen A. Wynn Institute for Vision Research, Department of Ophthalmology, Carver College of Medicine, University of Iowa, Iowa City, IA 52242.
  • Zhang F; McGovern Institute for Brain Research, Massachusetts Institute of Technology, Cambridge, MA 02142.
  • Clark AF; North Texas Eye Research Institute, University of North Texas Health Science Center, Fort Worth, TX 76107.
  • Sheffield VC; Department of Pediatrics, Carver College of Medicine, University of Iowa, Iowa City, IA 52242; gulab.zode@unthsc.edu val-sheffield@uiowa.edu.
Proc Natl Acad Sci U S A ; 114(42): 11199-11204, 2017 10 17.
Article em En | MEDLINE | ID: mdl-28973933

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Glicoproteínas / Terapia Genética / Glaucoma de Ângulo Aberto / Proteínas do Citoesqueleto / Proteínas do Olho / Sistemas CRISPR-Cas / Edição de Genes Tipo de estudo: Evaluation_studies / Prognostic_studies / Risk_factors_studies Limite: Animals / Humans Idioma: En Revista: Proc Natl Acad Sci U S A Ano de publicação: 2017 Tipo de documento: Article País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Glicoproteínas / Terapia Genética / Glaucoma de Ângulo Aberto / Proteínas do Citoesqueleto / Proteínas do Olho / Sistemas CRISPR-Cas / Edição de Genes Tipo de estudo: Evaluation_studies / Prognostic_studies / Risk_factors_studies Limite: Animals / Humans Idioma: En Revista: Proc Natl Acad Sci U S A Ano de publicação: 2017 Tipo de documento: Article País de publicação: Estados Unidos