Search details
1.
Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B.
N Engl J Med
; 388(8): 706-718, 2023 02 23.
Article
in English
| MEDLINE | ID: mdl-36812434
2.
Adeno-associated viruses for gene therapy - clinical implications and liver-related complications, a guide for hepatologists.
J Hepatol
; 80(2): 352-361, 2024 Feb.
Article
in English
| MEDLINE | ID: mdl-37890721
3.
Gene Therapy for Hemophilia B: Achievements, Open Issues, and Perspectives.
Semin Thromb Hemost
; 2024 May 31.
Article
in English
| MEDLINE | ID: mdl-38821066
4.
Which patients should be considered for gene therapy.
J Viral Hepat
; 31 Suppl 1: 9-13, 2024 04.
Article
in English
| MEDLINE | ID: mdl-38606942
5.
Next-generation strategies to improve safety and efficacy of adeno-associated virus-based gene therapy for hemophilia: lessons from clinical trials in other gene therapies.
Haematologica
; 2024 Mar 07.
Article
in English
| MEDLINE | ID: mdl-38450517
6.
Current and emerging gene therapies for haemophilia A and B.
Haemophilia
; 30 Suppl 3: 12-20, 2024 Apr.
Article
in English
| MEDLINE | ID: mdl-38528615
7.
Eptacog beta for the management of patients with haemophilia A and B with inhibitors: A European perspective.
Haemophilia
; 30(2): 257-266, 2024 Mar.
Article
in English
| MEDLINE | ID: mdl-38317441
8.
Transitioning from emicizumab prophylaxis to valoctocogene roxaparvovec gene therapy: A simulation study for individuals with severe haemophilia A.
Haemophilia
; 2024 Apr 29.
Article
in English
| MEDLINE | ID: mdl-38684460
9.
The current challenges faced by people with hemophilia B.
Eur J Haematol
; 112(3): 339-349, 2024 Mar.
Article
in English
| MEDLINE | ID: mdl-38082533
10.
Gene therapy for hemophilia: a review on clinical benefit, limitations, and remaining issues.
Blood
; 138(11): 923-931, 2021 09 16.
Article
in English
| MEDLINE | ID: mdl-34232980
11.
Endothelial dysfunction and atherosclerosis related miRNA-expression in patients with haemophilia.
Haemophilia
; 29(1): 61-71, 2023 Jan.
Article
in English
| MEDLINE | ID: mdl-36112753
12.
Accreditation model of European Haemophilia Centres in the era of novel treatments and gene therapy.
Haemophilia
; 29(6): 1442-1449, 2023 Nov.
Article
in English
| MEDLINE | ID: mdl-37819168
13.
Early-onset venous thromboembolisms in newly diagnosed non-promyelocytic acute myeloid leukemia patients undergoing intensive induction chemotherapy.
Eur J Haematol
; 110(4): 426-434, 2023 Apr.
Article
in English
| MEDLINE | ID: mdl-36573351
14.
Prophylaxis with recombinant von Willebrand factor in patients with type 3 von Willebrand disease: Results of a post hoc analysis from a phase 3 trial.
Eur J Haematol
; 111(1): 29-40, 2023 Jul.
Article
in English
| MEDLINE | ID: mdl-36823994
15.
Bleeding and response to hemostatic therapy in acquired hemophilia A: results from the GTH-AH 01/2010 study.
Blood
; 136(3): 279-287, 2020 07 16.
Article
in English
| MEDLINE | ID: mdl-32268359
16.
Electronic diaries in the management of haemophilia gene therapy: Perspective of an expert group from the German, Austrian and Swiss Society on Thrombosis and Haemostasis (GTH).
Haemophilia
; 28(2): 264-269, 2022 Mar.
Article
in English
| MEDLINE | ID: mdl-35182445
17.
Intracranial hemorrhage in newly diagnosed non-promyelocytic acute myeloid leukemia patients admitted for intensive induction chemotherapy.
Eur J Haematol
; 108(2): 125-132, 2022 Feb.
Article
in English
| MEDLINE | ID: mdl-34714547
18.
Direct oral anticoagulants vs. low-molecular-weight heparin for pulmonary embolism in patients with glioblastoma.
Neurosurg Rev
; 45(1): 451-457, 2022 Feb.
Article
in English
| MEDLINE | ID: mdl-33900495
19.
Biomarkers and immunological parameters in haemophilia and rheumatoid arthritis patients: a comparative multiplexing laboratory study.
Haemophilia
; 27(1): e119-e126, 2021 Jan.
Article
in English
| MEDLINE | ID: mdl-33210410
20.
Delivery of AAV-based gene therapy through haemophilia centres-A need for re-evaluation of infrastructure and comprehensive care: A Joint publication of EAHAD and EHC.
Haemophilia
; 27(6): 967-973, 2021 Nov.
Article
in English
| MEDLINE | ID: mdl-34553460