Search details
1.
Prevention of recurrent thrombotic events in children with central venous catheter-associated venous thrombosis.
Blood
; 139(3): 452-460, 2022 01 20.
Article
in English
| MEDLINE | ID: mdl-34727184
2.
Rate of thrombosis in children and adolescents hospitalized with COVID-19 or MIS-C.
Blood
; 138(2): 190-198, 2021 07 15.
Article
in English
| MEDLINE | ID: mdl-33895804
3.
Treatment of venous thromboembolism in pediatric patients.
Blood
; 135(5): 335-343, 2020 01 30.
Article
in English
| MEDLINE | ID: mdl-31917400
4.
A novel MBTPS2 variant associated with BRESHECK syndrome impairs sterol-regulated transcription and the endoplasmic reticulum stress response.
Am J Med Genet A
; 188(2): 463-472, 2022 02.
Article
in English
| MEDLINE | ID: mdl-34655156
5.
Thrombotic events in critically ill children with coronavirus disease 2019 or multisystem inflammatory syndrome in children.
Curr Opin Pediatr
; 34(3): 261-267, 2022 06 01.
Article
in English
| MEDLINE | ID: mdl-35634699
6.
Thromboembolic prevention and anticoagulant therapy during the COVID-19 pandemic: updated clinical guidance from the anticoagulation forum.
J Thromb Thrombolysis
; 54(2): 197-210, 2022 Aug.
Article
in English
| MEDLINE | ID: mdl-35579732
7.
Efficacy of Early Prophylaxis Against Catheter-Associated Thrombosis in Critically Ill Children: A Bayesian Phase 2b Randomized Clinical Trial.
Crit Care Med
; 49(3): e235-e246, 2021 03 01.
Article
in English
| MEDLINE | ID: mdl-33372745
8.
Age-Dependent Heterogeneity in the Efficacy of Prophylaxis With Enoxaparin Against Catheter-Associated Thrombosis in Critically Ill Children: A Post Hoc Analysis of a Bayesian Phase 2b Randomized Clinical Trial.
Crit Care Med
; 49(4): e369-e380, 2021 04 01.
Article
in English
| MEDLINE | ID: mdl-33566465
9.
Real-world cost estimates of initiating emicizumab in US patients with haemophilia A.
Haemophilia
; 27(4): 591-598, 2021 Jul.
Article
in English
| MEDLINE | ID: mdl-34050689
10.
Venous Thromboembolism in Pediatric Inflammatory Bowel Disease: A Case-Control Study.
J Pediatr Gastroenterol Nutr
; 72(5): 742-747, 2021 05 01.
Article
in English
| MEDLINE | ID: mdl-33605670
11.
Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B.
Mol Ther
; 28(9): 2073-2082, 2020 09 02.
Article
in English
| MEDLINE | ID: mdl-32559433
12.
Real-world use of emicizumab in patients with haemophilia A: Bleeding outcomes and surgical procedures.
Haemophilia
; 26(4): 631-636, 2020 Jul.
Article
in English
| MEDLINE | ID: mdl-32311809
13.
Implantable venous access devices in children with severe hemophilia: a tertiary pediatric institutional experience.
Pediatr Radiol
; 50(8): 1148-1155, 2020 07.
Article
in English
| MEDLINE | ID: mdl-32390060
14.
Regional variation and cost implications of prescribed extended half-life factor concentrates among U.S. Haemophilia Treatment Centres for patients with moderate and severe haemophilia.
Haemophilia
; 25(4): 668-675, 2019 Jul.
Article
in English
| MEDLINE | ID: mdl-30993845
15.
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.
Lancet
; 390(10097): 849-860, 2017 Aug 26.
Article
in English
| MEDLINE | ID: mdl-28712537
16.
Letter to the Editor in Response to "Coagulation Abnormalities and Clinical Complications in Children With SARS-CoV-2: A Systematic Review of 48,322 Patients" Published in December 2021.
J Pediatr Hematol Oncol
; 45(1): 44-45, 2023 01 01.
Article
in English
| MEDLINE | ID: mdl-35973085
17.
A survey of pediatric hematology/oncology specialists regarding management of central line associated venous thrombosis.
Pediatr Blood Cancer
; 64(7)2017 Jul.
Article
in English
| MEDLINE | ID: mdl-27905682
18.
Andexanet alfa for reversal of rivaroxaban in a child with intracranial hemorrhage.
Pediatr Blood Cancer
; 69(6): e29484, 2022 06.
Article
in English
| MEDLINE | ID: mdl-34811876
19.
Endovascular Thrombolysis in the Management of Iliofemoral Thrombosis in Children: A Multi-Institutional Experience.
J Vasc Interv Radiol
; 27(4): 524-30, 2016 Apr.
Article
in English
| MEDLINE | ID: mdl-26944359
20.
IVC filter retrieval in adolescents: experience in a tertiary pediatric center.
Pediatr Radiol
; 46(4): 534-40, 2016 Apr.
Article
in English
| MEDLINE | ID: mdl-26795617