Search details
1.
A human genome editing-based MLL::AF4 ALL model recapitulates key cellular and molecular leukemogenic features.
Blood
; 142(20): 1752-1756, 2023 Nov 16.
Article
in English
| MEDLINE | ID: mdl-37756522
2.
Targeted gene therapy into a safe harbor site in human hematopoietic progenitor cells.
Gene Ther
; 27(9): 435-450, 2020 09.
Article
in English
| MEDLINE | ID: mdl-32218505
3.
Mitapivat versus Placebo for Pyruvate Kinase Deficiency.
N Engl J Med
; 386(26): 2538-2539, 2022 06 30.
Article
in English
| MEDLINE | ID: mdl-35767453
4.
Advances in the gene therapy of monogenic blood cell diseases.
Clin Genet
; 97(1): 89-102, 2020 01.
Article
in English
| MEDLINE | ID: mdl-31231794
5.
Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34+ cells from Fanconi anemia patients.
Blood
; 130(13): 1535-1542, 2017 09 28.
Article
in English
| MEDLINE | ID: mdl-28801449
6.
Comprehensive characterization of a novel, oncogenic and targetable SEPTIN6::ABL2 fusion in T-ALL.
Br J Haematol
; 202(3): 693-698, 2023 08.
Article
in English
| MEDLINE | ID: mdl-37264982
7.
Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency.
Mol Ther
; 24(7): 1187-98, 2016 08.
Article
in English
| MEDLINE | ID: mdl-27138040
8.
The NFKB Inducing Kinase Modulates Hematopoiesis During Stress.
Stem Cells
; 33(9): 2825-37, 2015 Sep.
Article
in English
| MEDLINE | ID: mdl-26037670
9.
Brief report: reduced expression of CD18 leads to the in vivo expansion of hematopoietic stem cells in mouse bone marrow.
Stem Cells
; 32(10): 2794-8, 2014 Oct.
Article
in English
| MEDLINE | ID: mdl-24906078
10.
Reticulocyte-prone malaria parasites predominantly invade CD71hi immature cells: implications for the development of an in vitro culture for Plasmodium vivax.
Malar J
; 12: 434, 2013 Dec 01.
Article
in English
| MEDLINE | ID: mdl-24289105
11.
In comparison with palm oil, dietary nut supplementation delays the progression of atherosclerotic lesions in female apoE-deficient mice.
Br J Nutr
; 109(2): 202-9, 2013 Jan 28.
Article
in English
| MEDLINE | ID: mdl-23302442
12.
Long-term skin regeneration in xenografts from iPSC teratoma-derived human keratinocytes.
Exp Dermatol
; 25(9): 736-8, 2016 09.
Article
in English
| MEDLINE | ID: mdl-27095005
13.
The Current Status of Mesenchymal Stromal Cells: Controversies, Unresolved Issues and Some Promising Solutions to Improve Their Therapeutic Efficacy.
Front Cell Dev Biol
; 9: 650664, 2021.
Article
in English
| MEDLINE | ID: mdl-33796536
14.
Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposes.
Mol Ther Methods Clin Dev
; 22: 66-75, 2021 Sep 10.
Article
in English
| MEDLINE | ID: mdl-34485595
15.
Increased intraocular insulin-like growth factor-I triggers blood-retinal barrier breakdown.
J Biol Chem
; 284(34): 22961-9, 2009 Aug 21.
Article
in English
| MEDLINE | ID: mdl-19473988
16.
In vivo proliferation advantage of genetically corrected hematopoietic stem cells in a mouse model of Fanconi anemia FA-D1.
Blood
; 112(13): 4853-61, 2008 Dec 15.
Article
in English
| MEDLINE | ID: mdl-18812474
17.
Rescue of pyruvate kinase deficiency in mice by gene therapy using the human isoenzyme.
Mol Ther
; 17(12): 2000-9, 2009 Dec.
Article
in English
| MEDLINE | ID: mdl-19755962
18.
Lentiviral-mediated genetic correction of hematopoietic and mesenchymal progenitor cells from Fanconi anemia patients.
Mol Ther
; 17(6): 1083-92, 2009 Jun.
Article
in English
| MEDLINE | ID: mdl-19277017
19.
IKKß overexpression together with a lack of tumour suppressor genes causes ameloblastic odontomas in mice.
Int J Oral Sci
; 12(1): 1, 2020 01 02.
Article
in English
| MEDLINE | ID: mdl-31900382
20.
Evolution to pathogenicity of the parvovirus minute virus of mice in immunodeficient mice involves genetic heterogeneity at the capsid domain that determines tropism.
J Virol
; 82(3): 1195-203, 2008 Feb.
Article
in English
| MEDLINE | ID: mdl-18045943