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1.
GLA-modified RNA treatment lowers GB3 levels in iPSC-derived cardiomyocytes from Fabry-affected individuals.
Am J Hum Genet
; 110(9): 1600-1605, 2023 09 07.
Article
in English
| MEDLINE | ID: mdl-37607539
2.
The Effect of Fabry Disease Therapy on Bone Mineral Density.
Diseases
; 12(5)2024 May 13.
Article
in English
| MEDLINE | ID: mdl-38785757
3.
Cardiovascular outcomes in Fabry disease are linked to severity of chronic kidney disease.
Heart
; 101(4): 287-93, 2015 Feb.
Article
in English
| MEDLINE | ID: mdl-25381325
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