Search details
1.
Primary prophylaxis in children with severe haemophilia A and B-Implementation over the last 20 years as illustrated in real-world data in the PedNet cohorts.
Haemophilia
; 29(2): 498-504, 2023 Mar.
Article
in English
| MEDLINE | ID: mdl-36571801
2.
Hemostasis - A Balancing Act.
N Engl J Med
; 389(9): 853-856, 2023 Aug 31.
Article
in English
| MEDLINE | ID: mdl-37646683
3.
Inhibitor development in previously untreated patients with severe haemophilia: A comparison of included patients and outcomes between a clinical study and a registry-based study.
Haemophilia
; 26(5): 809-816, 2020 Sep.
Article
in English
| MEDLINE | ID: mdl-32627880
4.
Registries supporting new drug applications.
Pharmacoepidemiol Drug Saf
; 26(12): 1451-1457, 2017 Dec.
Article
in English
| MEDLINE | ID: mdl-28983992
5.
Factor VIII products and inhibitor development in severe hemophilia A.
N Engl J Med
; 368(3): 231-9, 2013 Jan 17.
Article
in English
| MEDLINE | ID: mdl-23323899
6.
Timing of inhibitor development in more than 1000 previously untreated patients with severe hemophilia A.
Blood
; 134(3): 317-320, 2019 07 18.
Article
in English
| MEDLINE | ID: mdl-31186271
7.
Different impact of factor VIII products on inhibitor development?
Thromb J
; 14(Suppl 1): 31, 2016.
Article
in English
| MEDLINE | ID: mdl-27766057
8.
A Cure for Hemophilia within Reach.
N Engl J Med
; 377(26): 2592-2593, 2017 12 28.
Article
in English
| MEDLINE | ID: mdl-29224412
9.
Assessment of clotting factor concentrates--pivotal studies and long-term requirements.
Semin Thromb Hemost
; 41(8): 855-9, 2015 Nov.
Article
in English
| MEDLINE | ID: mdl-26479895
10.
Correlation between phenotype and genotype in a large unselected cohort of children with severe hemophilia A.
Blood
; 121(19): 3946-52, S1, 2013 May 09.
Article
in English
| MEDLINE | ID: mdl-23482934
11.
Intermediate-dose versus high-dose prophylaxis for severe hemophilia: comparing outcome and costs since the 1970s.
Blood
; 122(7): 1129-36, 2013 Aug 15.
Article
in English
| MEDLINE | ID: mdl-23777770
12.
Intensity of factor VIII treatment and inhibitor development in children with severe hemophilia A: the RODIN study.
Blood
; 121(20): 4046-55, 2013 May 16.
Article
in English
| MEDLINE | ID: mdl-23553768
13.
WFH Guidelines for the Management of Hemophilia, 3rd edition.
Haemophilia
; 26 Suppl 6: 1-158, 2020 Aug.
Article
in English
| MEDLINE | ID: mdl-32744769
14.
F8 gene mutation type and inhibitor development in patients with severe hemophilia A: systematic review and meta-analysis.
Blood
; 119(12): 2922-34, 2012 Mar 22.
Article
in English
| MEDLINE | ID: mdl-22282501
15.
Can a "center effect" explain the higher frequency of inhibitors for a second-generation recombinant factor VIII product?
Blood
; 126(18): 2164-5, 2015 Oct 29.
Article
in English
| MEDLINE | ID: mdl-26392597
16.
Factor VIII products and inhibitors in severe hemophilia A.
N Engl J Med
; 368(15): 1457, 2013 04 11.
Article
in English
| MEDLINE | ID: mdl-23574131
17.
A modeling approach to evaluate long-term outcome of prophylactic and on demand treatment strategies for severe hemophilia A.
Haematologica
; 96(5): 738-43, 2011 May.
Article
in English
| MEDLINE | ID: mdl-21273268
18.
Capturing Data in Rare Disease Registries to Support Regulatory Decision Making: A Survey Study Among Industry and Other Stakeholders.
Drug Saf
; 44(8): 853-861, 2021 08.
Article
in English
| MEDLINE | ID: mdl-34091881
19.
Macrophages contribute to the cellular uptake of von Willebrand factor and factor VIII in vivo.
Blood
; 112(5): 1704-12, 2008 Sep 01.
Article
in English
| MEDLINE | ID: mdl-18559674
20.
Factor VIII-specific B cell responses in haemophilia A patients with inhibitors.
Haemophilia
; 16(102): 35-43, 2010 May.
Article
in English
| MEDLINE | ID: mdl-20536984