Detalles de la búsqueda
1.
Assessing perspectives of disease burden and clinically meaningful changes using the Spinal Muscular Atrophy Health Index in adolescents and young adults.
Muscle Nerve
; 66(3): 276-281, 2022 09.
Artículo
en Inglés
| MEDLINE | ID: mdl-35616549
2.
Understanding the relationship between the 32-item motor function measure and daily activities from an individual with spinal muscular atrophy and their caregivers' perspective: a two-part study.
BMC Neurol
; 21(1): 143, 2021 Mar 31.
Artículo
en Inglés
| MEDLINE | ID: mdl-33789607
3.
Awareness screening and referral patterns among pediatricians in the United States related to early clinical features of spinal muscular atrophy (SMA).
BMC Pediatr
; 21(1): 236, 2021 05 17.
Artículo
en Inglés
| MEDLINE | ID: mdl-34001052
4.
Six-minute walk test is reliable and valid in spinal muscular atrophy.
Muscle Nerve
; 54(5): 836-842, 2016 11.
Artículo
en Inglés
| MEDLINE | ID: mdl-27015431
5.
Rasch analysis of the Pediatric Evaluation of Disability Inventory-computer adaptive test (PEDI-CAT) item bank for children and young adults with spinal muscular atrophy.
Muscle Nerve
; 54(6): 1097-1107, 2016 12.
Artículo
en Inglés
| MEDLINE | ID: mdl-27121348
6.
Correction to: Understanding the relationship between the 32-item motor function measure and daily activities from an individual with spinal muscular atrophy and their caregivers' perspective: a two-part study.
BMC Neurol
; 21(1): 354, 2021 Sep 13.
Artículo
en Inglés
| MEDLINE | ID: mdl-34517827
7.
Assessment of Barriers to Referral and Appointment Wait Times for the Evaluation of Spinal Muscular Atrophy (SMA): Findings from a Web-Based Physician Survey.
Neurol Ther
; 13(3): 583-598, 2024 Jun.
Artículo
en Inglés
| MEDLINE | ID: mdl-38430355
8.
Clinical and Research Readiness for Spinal Muscular Atrophy: The Time Is Now for Knowledge Translation.
Phys Ther
; 102(10)2022 10 06.
Artículo
en Inglés
| MEDLINE | ID: mdl-35904447
9.
The Cure SMA Clinical Trial Experience Survey: A Study of Trial Participant Perspectives on Clinical Trial Management and Patient-Centric Management Practices.
Neurol Ther
; 11(3): 1167-1181, 2022 Sep.
Artículo
en Inglés
| MEDLINE | ID: mdl-35635603
10.
"I have SMA, SMA doesn't have me": a qualitative snapshot into the challenges, successes, and quality of life of adolescents and young adults with SMA.
Orphanet J Rare Dis
; 16(1): 96, 2021 02 22.
Artículo
en Inglés
| MEDLINE | ID: mdl-33618755
11.
A Patient-Centered Evaluation of Meaningful Change on the 32-Item Motor Function Measure in Spinal Muscular Atrophy Using Qualitative and Quantitative Data.
Front Neurol
; 12: 770423, 2021.
Artículo
en Inglés
| MEDLINE | ID: mdl-35111124
12.
The Cure SMA Membership Surveys: Highlights of Key Demographic and Clinical Characteristics of Individuals with Spinal Muscular Atrophy.
J Neuromuscul Dis
; 8(1): 109-123, 2021.
Artículo
en Inglés
| MEDLINE | ID: mdl-33104036
13.
Quality of life data for individuals affected by spinal muscular atrophy: a baseline dataset from the Cure SMA Community Update Survey.
Orphanet J Rare Dis
; 15(1): 217, 2020 08 24.
Artículo
en Inglés
| MEDLINE | ID: mdl-32838797
14.
Economic burden of spinal muscular atrophy: an analysis of claims data.
J Mark Access Health Policy
; 8(1): 1843277, 2020 Nov 08.
Artículo
en Inglés
| MEDLINE | ID: mdl-33224449
15.
The SMA Clinical Trial Readiness Program: creation and evaluation of a program to enhance SMA trial readiness in the United States.
Orphanet J Rare Dis
; 15(1): 118, 2020 05 22.
Artículo
en Inglés
| MEDLINE | ID: mdl-32443972
16.
Evaluating Benefit-risk Decision-making in Spinal Muscular Atrophy: A First-ever Study to Assess Risk Tolerance in the SMA Patient Community.
Clin Ther
; 41(5): 943-960.e4, 2019 05.
Artículo
en Inglés
| MEDLINE | ID: mdl-31056304
17.
Single-Blind, Randomized, Controlled Clinical Trial of Exercise in Ambulatory Spinal Muscular Atrophy: Why are the Results Negative?
J Neuromuscul Dis
; 2(4): 463-470, 2015 Oct 07.
Artículo
en Inglés
| MEDLINE | ID: mdl-27858749
Resultados
1 -
17
de 17
1
Próxima >
>>