Detalles de la búsqueda
1.
Long-term efficacy and safety results of taliglucerase alfa through 5years in adult treatment-naïve patients with Gaucher disease.
Blood Cells Mol Dis
; 78: 14-21, 2019 09.
Artículo
en Inglés
| MEDLINE | ID: mdl-27499018
2.
Outcomes after 8 years of eliglustat therapy for Gaucher disease type 1: Final results from the Phase 2 trial.
Am J Hematol
; 94(1): 29-38, 2019 01.
Artículo
en Inglés
| MEDLINE | ID: mdl-30264864
3.
The role of high density lipoprotein in Type 1 Gaucher disease.
Blood Cells Mol Dis
; 68: 43-46, 2018 02.
Artículo
en Inglés
| MEDLINE | ID: mdl-27876360
4.
Azacitidine-lenalidomide (ViLen) combination yields a high response rate in higher risk myelodysplastic syndromes (MDS)-ViLen-01 protocol.
Ann Hematol
; 95(11): 1811-8, 2016 Oct.
Artículo
en Inglés
| MEDLINE | ID: mdl-27546027
5.
Enzyme replacement therapy with taliglucerase alfa: 36-month safety and efficacy results in adult patients with Gaucher disease previously treated with imiglucerase.
Am J Hematol
; 91(7): 661-5, 2016 07.
Artículo
en Inglés
| MEDLINE | ID: mdl-27102949
6.
Long-term efficacy and safety results of taliglucerase alfa up to 36 months in adult treatment-naïve patients with Gaucher disease.
Am J Hematol
; 91(7): 656-60, 2016 07.
Artículo
en Inglés
| MEDLINE | ID: mdl-27174694
7.
Impaired migration capacity in monocytes derived from patients with Gaucher disease.
Blood Cells Mol Dis
; 55(2): 180-6, 2015 Aug.
Artículo
en Inglés
| MEDLINE | ID: mdl-25564295
8.
The road to biosimilars in rare diseases - ongoing lessons from Gaucher disease.
Am J Hematol
; 95(3): 233-237, 2020 03.
Artículo
en Inglés
| MEDLINE | ID: mdl-31816110
9.
A Phase 3, multicenter, open-label, switchover trial to assess the safety and efficacy of taliglucerase alfa, a plant cell-expressed recombinant human glucocerebrosidase, in adult and pediatric patients with Gaucher disease previously treated with imiglucerase.
Blood Cells Mol Dis
; 53(4): 253-60, 2014 Dec.
Artículo
en Inglés
| MEDLINE | ID: mdl-24950666
10.
Eliglustat, an investigational oral therapy for Gaucher disease type 1: Phase 2 trial results after 4 years of treatment.
Blood Cells Mol Dis
; 53(4): 274-6, 2014 Dec.
Artículo
en Inglés
| MEDLINE | ID: mdl-24835462
11.
Addendum to Letter to the Editor: Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1.
Blood Cells Mol Dis
; 77: 101-102, 2019 07.
Artículo
en Inglés
| MEDLINE | ID: mdl-31029022
12.
Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat.
Skeletal Radiol
; 43(10): 1353-60, 2014 Oct.
Artículo
en Inglés
| MEDLINE | ID: mdl-24816856
13.
Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1.
Blood Cells Mol Dis
; 71: 71-74, 2018 07.
Artículo
en Inglés
| MEDLINE | ID: mdl-29680197
14.
Hypercoagulability, parkinsonism, and Gaucher disease.
Semin Thromb Hemost
; 39(8): 928-34, 2013 Nov.
Artículo
en Inglés
| MEDLINE | ID: mdl-24129683
15.
Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease.
Blood
; 118(22): 5767-73, 2011 Nov 24.
Artículo
en Inglés
| MEDLINE | ID: mdl-21900191
16.
Real-World Experiences with Taliglucerase Alfa Home Infusions for Patients with Gaucher Disease: A Global Cohort Study.
J Clin Med
; 12(18)2023 Sep 12.
Artículo
en Inglés
| MEDLINE | ID: mdl-37762854
17.
MDS-Related Anemia Is Associated with Impaired Quality of Life but Improvement Is Not Always Achieved by Increased Hemoglobin Level.
J Clin Med
; 12(18)2023 Sep 09.
Artículo
en Inglés
| MEDLINE | ID: mdl-37762806
18.
Improvement in hematological, visceral, and skeletal manifestations of Gaucher disease type 1 with oral eliglustat tartrate (Genz-112638) treatment: 2-year results of a phase 2 study.
Blood
; 116(20): 4095-8, 2010 Nov 18.
Artículo
en Inglés
| MEDLINE | ID: mdl-20713962
19.
A phase 2 study of eliglustat tartrate (Genz-112638), an oral substrate reduction therapy for Gaucher disease type 1.
Blood
; 116(6): 893-9, 2010 Aug 12.
Artículo
en Inglés
| MEDLINE | ID: mdl-20439622
20.
A reappraisal of Gaucher disease-diagnosis and disease management algorithms.
Am J Hematol
; 86(1): 110-5, 2011 Jan.
Artículo
en Inglés
| MEDLINE | ID: mdl-21080341