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Duchenne Muscular Dystrophy Myogenic Cells from Urine-Derived Stem Cells Recapitulate the Dystrophin Genotype and Phenotype.
Falzarano, Maria Sofia; D'Amario, Domenico; Siracusano, Andrea; Massetti, Massimo; Amodeo, Antonio; La Neve, Federica; Maroni, Camilla Reina; Mercuri, Eugenio; Osman, Hana; Scotton, Chiara; Armaroli, Annarita; Rossi, Rachele; Selvatici, Rita; Crea, Filippo; Ferlini, Alessandra.
Afiliación
  • Falzarano MS; 1 UOL (Unità Operativa Logistica) of Medical Genetics, University of Ferrara , Ferrara, Italy.
  • D'Amario D; 2 Department of Cardiovascular Medicine, Catholic University of the Sacred Heart , Rome, Italy.
  • Siracusano A; 2 Department of Cardiovascular Medicine, Catholic University of the Sacred Heart , Rome, Italy.
  • Massetti M; 2 Department of Cardiovascular Medicine, Catholic University of the Sacred Heart , Rome, Italy.
  • Amodeo A; 3 Department of Cardiothoracic Surgery, Ospedale Bambino Gesù , Rome, Italy.
  • La Neve F; 2 Department of Cardiovascular Medicine, Catholic University of the Sacred Heart , Rome, Italy.
  • Maroni CR; 2 Department of Cardiovascular Medicine, Catholic University of the Sacred Heart , Rome, Italy.
  • Mercuri E; 4 Pediatric Neurology Unit, Catholic University, Rome , Italy.
  • Osman H; 1 UOL (Unità Operativa Logistica) of Medical Genetics, University of Ferrara , Ferrara, Italy.
  • Scotton C; 1 UOL (Unità Operativa Logistica) of Medical Genetics, University of Ferrara , Ferrara, Italy.
  • Armaroli A; 1 UOL (Unità Operativa Logistica) of Medical Genetics, University of Ferrara , Ferrara, Italy.
  • Rossi R; 1 UOL (Unità Operativa Logistica) of Medical Genetics, University of Ferrara , Ferrara, Italy.
  • Selvatici R; 1 UOL (Unità Operativa Logistica) of Medical Genetics, University of Ferrara , Ferrara, Italy.
  • Crea F; 2 Department of Cardiovascular Medicine, Catholic University of the Sacred Heart , Rome, Italy.
  • Ferlini A; 1 UOL (Unità Operativa Logistica) of Medical Genetics, University of Ferrara , Ferrara, Italy.
Hum Gene Ther ; 27(10): 772-783, 2016 10.
Article en En | MEDLINE | ID: mdl-27530229

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Distrofina / Oligonucleótidos Antisentido / Distrofia Muscular de Duchenne Límite: Humans Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2016 Tipo del documento: Article País de afiliación: Italia

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Distrofina / Oligonucleótidos Antisentido / Distrofia Muscular de Duchenne Límite: Humans Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2016 Tipo del documento: Article País de afiliación: Italia