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Patient-Specific iPSC-Derived Endothelial Cells Provide Long-Term Phenotypic Correction of Hemophilia A.
Olgasi, Cristina; Talmon, Maria; Merlin, Simone; Cucci, Alessia; Richaud-Patin, Yvonne; Ranaldo, Gabriella; Colangelo, Donato; Di Scipio, Federica; Berta, Giovanni N; Borsotti, Chiara; Valeri, Federica; Faraldi, Francesco; Prat, Maria; Messina, Maria; Schinco, Piercarla; Lombardo, Angelo; Raya, Angel; Follenzi, Antonia.
Afiliación
  • Olgasi C; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy.
  • Talmon M; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy.
  • Merlin S; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy.
  • Cucci A; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy.
  • Richaud-Patin Y; Center of Regenerative Medicine in Barcelona (CMRB), Hospital Durans Reynals, Hospitalet de Llobregat, 08908 Barcelona, Spain; Center for Networked Biomedical Research on Bioengineering, Biomaterials and Nanomedicine (CIBER-BBN), 28029 Madrid, Spain.
  • Ranaldo G; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy.
  • Colangelo D; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy.
  • Di Scipio F; Azienda Osp/Univ San Luigi Gonzaga, 10043 Orbassano, Italy.
  • Berta GN; Azienda Osp/Univ San Luigi Gonzaga, 10043 Orbassano, Italy.
  • Borsotti C; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy.
  • Valeri F; A.O.U. Città della Salute e della Scienza, 10126 Torino, Italy.
  • Faraldi F; SC Oculistica ASL TO5, 10100 Torino, Italy.
  • Prat M; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy.
  • Messina M; A.O.U. Città della Salute e della Scienza, 10126 Torino, Italy.
  • Schinco P; A.O.U. Città della Salute e della Scienza, 10126 Torino, Italy.
  • Lombardo A; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, Italy; San Raffaele Scientific Institute, 20132 Milan, Italy; Vita-Salute San Raffaele University, 20132 Milan, Italy.
  • Raya A; Center of Regenerative Medicine in Barcelona (CMRB), Hospital Durans Reynals, Hospitalet de Llobregat, 08908 Barcelona, Spain; Center for Networked Biomedical Research on Bioengineering, Biomaterials and Nanomedicine (CIBER-BBN), 28029 Madrid, Spain; Institució Catalana de Recerca i Estudis Avançats
  • Follenzi A; Department of Health Sciences, Università del Piemonte Orientale "A. Avogadro", 28100 Novara, Italy. Electronic address: antonia.follenzi@med.uniupo.it.
Stem Cell Reports ; 11(6): 1391-1406, 2018 12 11.
Article en En | MEDLINE | ID: mdl-30416049

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Células Endoteliales / Células Madre Pluripotentes Inducidas / Hemofilia A Tipo de estudio: Guideline / Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Stem Cell Reports Año: 2018 Tipo del documento: Article País de afiliación: Italia

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Células Endoteliales / Células Madre Pluripotentes Inducidas / Hemofilia A Tipo de estudio: Guideline / Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Stem Cell Reports Año: 2018 Tipo del documento: Article País de afiliación: Italia