Your browser doesn't support javascript.
loading
Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study.
Klopstock, Thomas; Tricta, Fernando; Neumayr, Lynne; Karin, Ivan; Zorzi, Giovanna; Fradette, Caroline; Kmiec, Tomasz; Büchner, Boriana; Steele, Hannah E; Horvath, Rita; Chinnery, Patrick F; Basu, Anna; Küpper, Clemens; Neuhofer, Christiane; Kálmán, Bernadette; Dusek, Petr; Yapici, Zuhal; Wilson, Ian; Zhao, Feng; Zibordi, Federica; Nardocci, Nardo; Aguilar, Christine; Hayflick, Susan J; Spino, Michael; Blamire, Andrew M; Hogarth, Penelope; Vichinsky, Elliott.
Afiliación
  • Klopstock T; Department of Neurology, Friedrich-Baur-Institute, Ludwig-Maximilians-University of Munich, Munich, Germany; German Center for Neurodegenerative Diseases, Munich, Germany; Munich Cluster for Systems Neurology, Munich, Germany. Electronic address: thomas.klopstock@med.lmu.de.
  • Tricta F; ApoPharma Inc, Toronto, ON, Canada.
  • Neumayr L; Department of Hematology Oncology, UCSF Benioff Children's Hospital and Research Center Oakland, Oakland, CA, USA.
  • Karin I; Department of Neurology, Friedrich-Baur-Institute, Ludwig-Maximilians-University of Munich, Munich, Germany.
  • Zorzi G; Department of Pediatric Neuroscience, Neurological Institute Carlo Besta, Milan, Italy.
  • Fradette C; ApoPharma Inc, Toronto, ON, Canada.
  • Kmiec T; Department of Neurology and Epileptology, Children's Memorial Health Institute, Warsaw, Poland.
  • Büchner B; Department of Neurology, Friedrich-Baur-Institute, Ludwig-Maximilians-University of Munich, Munich, Germany.
  • Steele HE; Institute of Genetic Medicine, Newcastle University, Newcastle upon Tyne, UK.
  • Horvath R; Institute of Genetic Medicine, Newcastle University, Newcastle upon Tyne, UK; Department of Clinical Neurosciences, Cambridge University, Cambridge, UK.
  • Chinnery PF; Department of Clinical Neurosciences, Cambridge University, Cambridge, UK.
  • Basu A; Institute of Neuroscience, Newcastle University, Newcastle upon Tyne, UK.
  • Küpper C; Department of Neurology, Friedrich-Baur-Institute, Ludwig-Maximilians-University of Munich, Munich, Germany.
  • Neuhofer C; Department of Neurology, Friedrich-Baur-Institute, Ludwig-Maximilians-University of Munich, Munich, Germany.
  • Kálmán B; Institute of Laboratory Medicine, Szentagothai Research Center, University of Pécs, Pécs, Hungary.
  • Dusek P; Charles University, Prague, Czech Republic.
  • Yapici Z; Department of Child Neurology, Istanbul Faculty of Medicine, Turkey.
  • Wilson I; Institute of Cellular Medicine and Newcastle Magnetic Resonance Centre, Newcastle University, Newcastle upon Tyne, UK.
  • Zhao F; ApoPharma Inc, Toronto, ON, Canada.
  • Zibordi F; Department of Pediatric Neuroscience, Neurological Institute Carlo Besta, Milan, Italy.
  • Nardocci N; Department of Pediatric Neuroscience, Neurological Institute Carlo Besta, Milan, Italy.
  • Aguilar C; Pediatric Rehabilitation Department, UCSF Benioff Children's Hospital and Research Center Oakland, Oakland, CA, USA.
  • Hayflick SJ; Department of Molecular & Medical Genetics, Oregon Health and Science University, Portland, OR, USA.
  • Spino M; ApoPharma Inc, Toronto, ON, Canada.
  • Blamire AM; Institute of Cellular Medicine and Newcastle Magnetic Resonance Centre, Newcastle University, Newcastle upon Tyne, UK.
  • Hogarth P; Department of Molecular & Medical Genetics, Oregon Health and Science University, Portland, OR, USA.
  • Vichinsky E; Department of Hematology Oncology, UCSF Benioff Children's Hospital and Research Center Oakland, Oakland, CA, USA.
Lancet Neurol ; 18(7): 631-642, 2019 07.
Article en En | MEDLINE | ID: mdl-31202468
Asunto(s)
Texto completo
Imprimir
XML
PubMed Links
Buscar en Google

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Quelantes del Hierro / Deferiprona / Neurodegeneración Asociada a Pantotenato Quinasa Tipo de estudio: Clinical_trials / Risk_factors_studies Límite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Male / Middle aged Idioma: En Revista: Lancet Neurol Asunto de la revista: NEUROLOGIA Año: 2019 Tipo del documento: Article
Texto completo
Imprimir
XML
PubMed Links
Buscar en Google

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Quelantes del Hierro / Deferiprona / Neurodegeneración Asociada a Pantotenato Quinasa Tipo de estudio: Clinical_trials / Risk_factors_studies Límite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Male / Middle aged Idioma: En Revista: Lancet Neurol Asunto de la revista: NEUROLOGIA Año: 2019 Tipo del documento: Article