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Assessment of Treatment Effect With Multiple Outcomes in 2 Clinical Trials of Patients With Duchenne Muscular Dystrophy.
Li, Daniel; McDonald, Craig M; Elfring, Gary L; Souza, Marcio; McIntosh, Joseph; Kim, Dae Hyun; Wei, Lee-Jen.
Afiliación
  • Li D; Department of Biostatistics, Harvard T.H. Chan School of Public Health, Boston, Massachusetts.
  • McDonald CM; Department of Physical Medicine and Rehabilitation, Department of Pediatrics, University of California Davis, Sacramento.
  • Elfring GL; PTC Therapeutics, South Plainfield, New Jersey.
  • Souza M; PTC Therapeutics, South Plainfield, New Jersey.
  • McIntosh J; PTC Therapeutics, South Plainfield, New Jersey.
  • Kim DH; Hinda and Arthur Marcus Institute for Aging Research, Hebrew SeniorLife, Harvard Medical School, Boston, Massachusetts.
  • Wei LJ; Department of Biostatistics, Harvard T.H. Chan School of Public Health, Boston, Massachusetts.
JAMA Netw Open ; 3(2): e1921306, 2020 02 05.
Article en En | MEDLINE | ID: mdl-32058550

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Oxadiazoles / Distrofia Muscular de Duchenne Tipo de estudio: Clinical_trials Límite: Humans Idioma: En Revista: JAMA Netw Open Año: 2020 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Oxadiazoles / Distrofia Muscular de Duchenne Tipo de estudio: Clinical_trials Límite: Humans Idioma: En Revista: JAMA Netw Open Año: 2020 Tipo del documento: Article