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Whole brain delivery of an instability-prone Mecp2 transgene improves behavioral and molecular pathological defects in mouse models of Rett syndrome.
Luoni, Mirko; Giannelli, Serena; Indrigo, Marzia Tina; Niro, Antonio; Massimino, Luca; Iannielli, Angelo; Passeri, Laura; Russo, Fabio; Morabito, Giuseppe; Calamita, Piera; Gregori, Silvia; Deverman, Benjamin; Broccoli, Vania.
Afiliación
  • Luoni M; Stem Cell and Neurogenesis Unit, Division of Neuroscience, San Raffaele Scientific Institute, Milan, Italy.
  • Giannelli S; CNR Institute of Neuroscience, Milan, Italy.
  • Indrigo MT; Stem Cell and Neurogenesis Unit, Division of Neuroscience, San Raffaele Scientific Institute, Milan, Italy.
  • Niro A; Stem Cell and Neurogenesis Unit, Division of Neuroscience, San Raffaele Scientific Institute, Milan, Italy.
  • Massimino L; Stem Cell and Neurogenesis Unit, Division of Neuroscience, San Raffaele Scientific Institute, Milan, Italy.
  • Iannielli A; CNR Institute of Neuroscience, Milan, Italy.
  • Passeri L; Stem Cell and Neurogenesis Unit, Division of Neuroscience, San Raffaele Scientific Institute, Milan, Italy.
  • Russo F; Stem Cell and Neurogenesis Unit, Division of Neuroscience, San Raffaele Scientific Institute, Milan, Italy.
  • Morabito G; CNR Institute of Neuroscience, Milan, Italy.
  • Calamita P; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), San Raffaele Scientific Institute IRCCS, Via Olgettina, Milan, Italy.
  • Gregori S; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), San Raffaele Scientific Institute IRCCS, Via Olgettina, Milan, Italy.
  • Deverman B; Stem Cell and Neurogenesis Unit, Division of Neuroscience, San Raffaele Scientific Institute, Milan, Italy.
  • Broccoli V; National Institute of Molecular Genetics (INGM), Milan, Italy.
Elife ; 92020 03 24.
Article en En | MEDLINE | ID: mdl-32207685

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Encéfalo / Síndrome de Rett / Proteína 2 de Unión a Metil-CpG / Mutación Límite: Animals Idioma: En Revista: Elife Año: 2020 Tipo del documento: Article País de afiliación: Italia

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Encéfalo / Síndrome de Rett / Proteína 2 de Unión a Metil-CpG / Mutación Límite: Animals Idioma: En Revista: Elife Año: 2020 Tipo del documento: Article País de afiliación: Italia