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Results of a phase 2 trial of an oral CXCR4 antagonist, mavorixafor, for treatment of WHIM syndrome.
Dale, David C; Firkin, Frank; Bolyard, Audrey Anna; Kelley, Merideth; Makaryan, Vahagn; Gorelick, Kenneth J; Ebrahim, Tarek; Garg, Varun; Tang, Weihua; Jiang, Honghua; Skerlj, Renato; Beaussant Cohen, Sarah.
Afiliación
  • Dale DC; Department of Medicine, University of Washington, Seattle, WA.
  • Firkin F; Department of Medicine and.
  • Bolyard AA; University of Washington, Severe Chronic Neutropenia International Registry, Seattle, WA; and.
  • Kelley M; University of Washington, Severe Chronic Neutropenia International Registry, Seattle, WA; and.
  • Makaryan V; Department of Medicine, University of Washington, Seattle, WA.
  • Gorelick KJ; Department of Medicine, University of Washington, Seattle, WA.
  • Ebrahim T; X4 Pharmaceuticals, Inc, Cambridge, MA.
  • Garg V; X4 Pharmaceuticals, Inc, Cambridge, MA.
  • Tang W; X4 Pharmaceuticals, Inc, Cambridge, MA.
  • Jiang H; X4 Pharmaceuticals, Inc, Cambridge, MA.
  • Skerlj R; X4 Pharmaceuticals, Inc, Cambridge, MA.
  • Beaussant Cohen S; X4 Pharmaceuticals, Inc, Cambridge, MA.
Blood ; 136(26): 2994-3003, 2020 12 24.
Article en En | MEDLINE | ID: mdl-32870250

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Bencimidazoles / Butilaminas / Verrugas / Receptores CXCR4 / Enfermedades de Inmunodeficiencia Primaria / Aminoquinolinas Tipo de estudio: Clinical_trials / Observational_studies Límite: Adolescent / Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Blood Año: 2020 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Bencimidazoles / Butilaminas / Verrugas / Receptores CXCR4 / Enfermedades de Inmunodeficiencia Primaria / Aminoquinolinas Tipo de estudio: Clinical_trials / Observational_studies Límite: Adolescent / Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Blood Año: 2020 Tipo del documento: Article