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Intracerebroventricular dosing of N-sulfoglucosamine sulfohydrolase in mucopolysaccharidosis IIIA mice reduces markers of brain lysosomal dysfunction.
Magat, Jenna; Jones, Samantha; Baridon, Brian; Agrawal, Vishal; Wong, Hio; Giaramita, Alexander; Mangini, Linley; Handyside, Britta; Vitelli, Catherine; Parker, Monica; Yeung, Natasha; Zhou, Yu; Pungor, Erno; Slabodkin, Ilya; Gorostiza, Olivia; Aguilera, Allora; Lo, Melanie J; Alcozie, Saida; Christianson, Terri M; Tiger, Pascale M N; Vincelette, Jon; Fong, Sylvia; Gil, Geuncheol; Hague, Chuck; Lawrence, Roger; Wendt, Daniel J; Lebowitz, Jonathan H; Bunting, Stuart; Bullens, Sherry; Crawford, Brett E; Roy, Sushmita M; Woloszynek, Josh C.
Afiliación
  • Magat J; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Jones S; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Baridon B; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Agrawal V; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Wong H; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Giaramita A; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Mangini L; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Handyside B; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Vitelli C; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Parker M; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Yeung N; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Zhou Y; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Pungor E; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Slabodkin I; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Gorostiza O; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Aguilera A; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Lo MJ; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Alcozie S; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Christianson TM; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Tiger PMN; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Vincelette J; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Fong S; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Gil G; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Hague C; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Lawrence R; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Wendt DJ; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Lebowitz JH; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Bunting S; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Bullens S; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Crawford BE; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Roy SM; Department of Process Sciences, BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Woloszynek JC; Department of Research, BioMarin Pharmaceutical Inc, Novato, California, USA. Electronic address: josh.woloszynek@gmail.com.
J Biol Chem ; 298(12): 102625, 2022 12.
Article en En | MEDLINE | ID: mdl-36306823

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Encefalopatías / Mucopolisacaridosis III Límite: Animals / Humans Idioma: En Revista: J Biol Chem Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Encefalopatías / Mucopolisacaridosis III Límite: Animals / Humans Idioma: En Revista: J Biol Chem Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos