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Fenfluramine treatment is associated with improvement in everyday executive function in preschool-aged children (<5 years) with Dravet syndrome: A critical period for early neurodevelopment.
Bishop, Kim I; Isquith, Peter K; Gioia, Gerard A; Knupp, Kelly G; Scheffer, Ingrid E; Nabbout, Rima; Specchio, Nicola; Sullivan, Joseph; Auvin, Stéphane; Helen Cross, J; Guerrini, Renzo; Farfel, Gail; Galer, Bradley S; Gammaitoni, Arnold R.
Afiliación
  • Bishop KI; Global Pharma Consultancy, LLC, Muncy, PA, USA. Electronic address: kib@globalpharmaconsultancy.com.
  • Isquith PK; Global Pharma Consultancy, LLC, Muncy, PA, USA; Boston Children's Hospital, Harvard Medical School, Boston, MA, USA.
  • Gioia GA; Global Pharma Consultancy, LLC, Muncy, PA, USA; Children's National Health System, Rockville, MD, USA.
  • Knupp KG; Children's Hospital Colorado, Aurora, CO, USA.
  • Scheffer IE; University of Melbourne, Austin and Royal Children's Hospitals, Florey Institute and Murdoch Children's Research Institute, Melbourne, Victoria, Australia.
  • Nabbout R; Reference Centre for Rare Epilepsies, Hôpital Universitaire Necker-Enfants Malades, APHP, Member of EPICARE, Institut Imagine, Université Paris Cité, Paris, France.
  • Specchio N; Rar Bambino Gesù Children's Hospital IRCCS, Rome, Italy.
  • Sullivan J; University of California San Francisco, Benioff Children's Hospital, San Francisco, CA, USA.
  • Auvin S; Robert Debré Children's Hospital, APHP, Université de Paris, Paris, France; Institut Universitaire de France (IUF), Paris, France.
  • Helen Cross J; UCL NIHR BRC Great Ormond Street Institute of Child Health, London, UK.
  • Guerrini R; Anna Meyer Children's Hospital, University of Florence, Florence, Italy.
  • Farfel G; Formerly Zogenix, Inc., now a part of UCB, Emeryville, CA, USA.
  • Galer BS; Formerly Zogenix, Inc., now a part of UCB, Emeryville, CA, USA.
  • Gammaitoni AR; Formerly Zogenix, Inc., now a part of UCB, Emeryville, CA, USA.
Epilepsy Behav ; 138: 108994, 2023 01.
Article en En | MEDLINE | ID: mdl-36463826

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Epilepsias Mioclónicas / Función Ejecutiva Tipo de estudio: Clinical_trials / Risk_factors_studies Límite: Child / Child, preschool / Humans Idioma: En Revista: Epilepsy Behav Asunto de la revista: CIENCIAS DO COMPORTAMENTO / NEUROLOGIA Año: 2023 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Epilepsias Mioclónicas / Función Ejecutiva Tipo de estudio: Clinical_trials / Risk_factors_studies Límite: Child / Child, preschool / Humans Idioma: En Revista: Epilepsy Behav Asunto de la revista: CIENCIAS DO COMPORTAMENTO / NEUROLOGIA Año: 2023 Tipo del documento: Article