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Improved intravenous lentiviral gene therapy based on endothelial-specific promoter-driven factor VIII expression for hemophilia A.
Gong, Jie; Yang, Rui; Zhou, Min; Chang, Lung-Ji.
Afiliación
  • Gong J; Chengdu Women's and Children's Central Hospital, School of Medicine, University of Electronic Science and Technology of China, Chengdu, 611731, China.
  • Yang R; School of Medicine, University of Electronic Science and Technology of China, Chengdu, 610054, China.
  • Zhou M; School of Medicine, University of Electronic Science and Technology of China, Chengdu, 610054, China.
  • Chang LJ; Chengdu Women's and Children's Central Hospital, School of Medicine, University of Electronic Science and Technology of China, Chengdu, 611731, China.
Mol Med ; 29(1): 74, 2023 06 12.
Article en En | MEDLINE | ID: mdl-37308845

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Factor VIII / Hemofilia A Límite: Animals / Humans Idioma: En Revista: Mol Med Asunto de la revista: BIOLOGIA MOLECULAR Año: 2023 Tipo del documento: Article País de afiliación: China

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Factor VIII / Hemofilia A Límite: Animals / Humans Idioma: En Revista: Mol Med Asunto de la revista: BIOLOGIA MOLECULAR Año: 2023 Tipo del documento: Article País de afiliación: China