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Directed Alternative Splicing in Nijmegen Breakage Syndrome: Proof of Principle Concerning Its Therapeutical Application.
Salewsky, Bastian; Hildebrand, Gabriele; Rothe, Susanne; Parplys, Ann Christin; Radszewski, Janina; Kieslich, Moritz; Wessendorf, Petra; Krenzlin, Harald; Borgmann, Kerstin; Nussenzweig, André; Sperling, Karl; Digweed, Martin.
Afiliação
  • Salewsky B; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
  • Hildebrand G; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
  • Rothe S; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
  • Parplys AC; Laboratory of Radiobiology and Experimental Radiation Oncology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Radszewski J; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
  • Kieslich M; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
  • Wessendorf P; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
  • Krenzlin H; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
  • Borgmann K; Laboratory of Radiobiology and Experimental Radiation Oncology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Nussenzweig A; Laboratory of Genome Integrity, National Cancer Institute, National Institute of Health, Besthesda, Maryland, USA.
  • Sperling K; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
  • Digweed M; Institute of Medical and Human Genetics, Charité - Universitätsmedizin Berlin, Berlin, Germany.
Mol Ther ; 24(1): 117-24, 2016 Feb.
Article em En | MEDLINE | ID: mdl-26265251

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Proteínas Nucleares / Oligonucleotídeos Antissenso / Deleção de Sequência / Processamento Alternativo / Proteínas de Ciclo Celular / Síndrome de Quebra de Nijmegen Limite: Animals / Child / Female / Humans / Middle aged Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Alemanha País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Proteínas Nucleares / Oligonucleotídeos Antissenso / Deleção de Sequência / Processamento Alternativo / Proteínas de Ciclo Celular / Síndrome de Quebra de Nijmegen Limite: Animals / Child / Female / Humans / Middle aged Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Alemanha País de publicação: Estados Unidos