Your browser doesn't support javascript.
loading
Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65.
Georgiadis, A; Duran, Y; Ribeiro, J; Abelleira-Hervas, L; Robbie, S J; Sünkel-Laing, B; Fourali, S; Gonzalez-Cordero, A; Cristante, E; Michaelides, M; Bainbridge, J W B; Smith, A J; Ali, R R.
Afiliação
  • Georgiadis A; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Duran Y; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Ribeiro J; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Abelleira-Hervas L; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Robbie SJ; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Sünkel-Laing B; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Fourali S; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Gonzalez-Cordero A; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Cristante E; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Michaelides M; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Bainbridge JW; NIHR Biomedical Research Centre at Moorfields Eye Hospital, London EC1V 2PD, UK.
  • Smith AJ; Department of Genetics, UCL Institute of Ophthalmology, London EC1V 9EL, UK.
  • Ali RR; NIHR Biomedical Research Centre at Moorfields Eye Hospital, London EC1V 2PD, UK.
Gene Ther ; 23(12): 857-862, 2016 12.
Article em En | MEDLINE | ID: mdl-27653967

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Dependovirus / Cis-trans-Isomerases / Amaurose Congênita de Leber / Vetores Genéticos Tipo de estudo: Prognostic_studies Limite: Animals / Female / Humans / Male Idioma: En Revista: Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Dependovirus / Cis-trans-Isomerases / Amaurose Congênita de Leber / Vetores Genéticos Tipo de estudo: Prognostic_studies Limite: Animals / Female / Humans / Male Idioma: En Revista: Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Reino Unido