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[Intrathecal Nursinersen Therapy in Children with Spinal Muscular Atrophy and Spinal Deformities]. / Intrathekale Nursinersen-Therapie bei Kindern mit Spinaler Muskelatrophie und Wirbelsäulendeformitäten.
Lorenz, Heiko M; Kühnle, Ingrid; Edler, Jan; Hobbiebrunken, Elke; Wilichowski, Ekkehard; Tsaknakis, Konstantinos; Wilken, Bernd; Braunschweig, Lena; Hell, Anna K.
Afiliação
  • Lorenz HM; Department of Trauma, Orthopaedic and Plastic Surgery, Pediatric Orthopaedics, University Medical Center Göttingen, Göttingen.
  • Kühnle I; Pediatric Hematology and Oncology, University Medical Center Göttingen, Göttingen.
  • Edler J; Pediatric Hematology and Oncology, University Medical Center Göttingen, Göttingen.
  • Hobbiebrunken E; Department of Pediatric Neurology, University Medical Center Göttingen, Göttingen.
  • Wilichowski E; Department of Pediatric Neurology, University Medical Center Göttingen, Göttingen.
  • Tsaknakis K; Department of Trauma, Orthopaedic and Plastic Surgery, Pediatric Orthopaedics, University Medical Center Göttingen, Göttingen.
  • Wilken B; Department of Pediatric Neurology, Klinikum Kassel GmbH, Kassel.
  • Braunschweig L; Department of Trauma, Orthopaedic and Plastic Surgery, Pediatric Orthopaedics, University Medical Center Göttingen, Göttingen.
  • Hell AK; Department of Trauma, Orthopaedic and Plastic Surgery, Pediatric Orthopaedics, University Medical Center Göttingen, Göttingen.
Klin Padiatr ; 230(4): 231-233, 2018 07.
Article em De | MEDLINE | ID: mdl-29378349

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Coluna Vertebral / Atrofia Muscular Espinal / Fármacos Neuromusculares Limite: Child / Humans Idioma: De Revista: Klin Padiatr Ano de publicação: 2018 Tipo de documento: Article País de publicação: Alemanha

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Coluna Vertebral / Atrofia Muscular Espinal / Fármacos Neuromusculares Limite: Child / Humans Idioma: De Revista: Klin Padiatr Ano de publicação: 2018 Tipo de documento: Article País de publicação: Alemanha