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Extensive Transduction and Enhanced Spread of a Modified AAV2 Capsid in the Non-human Primate CNS.
Naidoo, Jerusha; Stanek, Lisa M; Ohno, Kousaku; Trewman, Savanah; Samaranch, Lluis; Hadaczek, Piotr; O'Riordan, Catherine; Sullivan, Jennifer; San Sebastian, Waldy; Bringas, John R; Snieckus, Christopher; Mahmoodi, Amin; Mahmoodi, Amir; Forsayeth, John; Bankiewicz, Krystof S; Shihabuddin, Lamya S.
Afiliação
  • Naidoo J; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Stanek LM; CNS Genetic Diseases, Neuroscience Research TA, Sanofi, Framingham, MA, USA.
  • Ohno K; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Trewman S; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Samaranch L; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Hadaczek P; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • O'Riordan C; CNS Genetic Diseases, Neuroscience Research TA, Sanofi, Framingham, MA, USA.
  • Sullivan J; CNS Genetic Diseases, Neuroscience Research TA, Sanofi, Framingham, MA, USA.
  • San Sebastian W; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Bringas JR; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Snieckus C; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Mahmoodi A; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Mahmoodi A; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Forsayeth J; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA.
  • Bankiewicz KS; Interventional Neuro Center, Department of Neurological Surgery, University of California, San Francisco, San Francisco, CA, USA. Electronic address: krystof.bankiewicz@ucsf.edu.
  • Shihabuddin LS; CNS Genetic Diseases, Neuroscience Research TA, Sanofi, Framingham, MA, USA.
Mol Ther ; 26(10): 2418-2430, 2018 10 03.
Article em En | MEDLINE | ID: mdl-30057240

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Medula Espinal / Terapia Genética / Parvovirinae / Vetores Genéticos / Neurônios Limite: Animals / Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Estados Unidos País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Medula Espinal / Terapia Genética / Parvovirinae / Vetores Genéticos / Neurônios Limite: Animals / Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Estados Unidos País de publicação: Estados Unidos