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Highly Efficient and Marker-free Genome Editing of Human Pluripotent Stem Cells by CRISPR-Cas9 RNP and AAV6 Donor-Mediated Homologous Recombination.
Martin, Renata M; Ikeda, Kazuya; Cromer, M Kyle; Uchida, Nobuko; Nishimura, Toshinobu; Romano, Rosa; Tong, Andrew J; Lemgart, Viktor T; Camarena, Joab; Pavel-Dinu, Mara; Sindhu, Camille; Wiebking, Volker; Vaidyanathan, Sriram; Dever, Daniel P; Bak, Rasmus O; Laustsen, Anders; Lesch, Benjamin J; Jakobsen, Martin R; Sebastiano, Vittorio; Nakauchi, Hiromitsu; Porteus, Matthew H.
Afiliação
  • Martin RM; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Ikeda K; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Cromer MK; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Uchida N; ReGen Med Division, BOCO Silicon Valley, Palo Alto, CA 94303, USA.
  • Nishimura T; Department of Genetics, Stanford University, Stanford, CA 94305, USA.
  • Romano R; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Tong AJ; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Lemgart VT; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Camarena J; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Pavel-Dinu M; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Sindhu C; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Wiebking V; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Vaidyanathan S; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Dever DP; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Bak RO; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Laustsen A; Department of Biomedicine, Aarhus University, Wilhelm Meyers Alle 4, 8000 Aarhus C, Denmark; Aarhus Research Centre of Innate Immunology, Aarhus University, Wilhelm Meyers Alle 4, 8000 Aarhus C, Denmark.
  • Lesch BJ; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA.
  • Jakobsen MR; Department of Biomedicine, Aarhus University, Wilhelm Meyers Alle 4, 8000 Aarhus C, Denmark; Aarhus Research Centre of Innate Immunology, Aarhus University, Wilhelm Meyers Alle 4, 8000 Aarhus C, Denmark.
  • Sebastiano V; Department of Obstetrics & Gynecology, Stanford University, Stanford, CA 94305, USA.
  • Nakauchi H; Department of Genetics, Stanford University, Stanford, CA 94305, USA.
  • Porteus MH; Department of Pediatrics, Stanford University, Stanford, CA 94305, USA. Electronic address: mporteus@stanford.edu.
Cell Stem Cell ; 24(5): 821-828.e5, 2019 05 02.
Article em En | MEDLINE | ID: mdl-31051134

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Dependovirus / Células-Tronco Pluripotentes / Sistemas CRISPR-Cas / Proteína 9 Associada à CRISPR / Genótipo Tipo de estudo: Diagnostic_studies Limite: Humans Idioma: En Revista: Cell Stem Cell Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Estados Unidos País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Dependovirus / Células-Tronco Pluripotentes / Sistemas CRISPR-Cas / Proteína 9 Associada à CRISPR / Genótipo Tipo de estudo: Diagnostic_studies Limite: Humans Idioma: En Revista: Cell Stem Cell Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Estados Unidos País de publicação: Estados Unidos