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Nusinersen improves walking distance and reduces fatigue in later-onset spinal muscular atrophy.
Montes, Jacqueline; Dunaway Young, Sally; Mazzone, Elena S; Pasternak, Amy; Glanzman, Allan M; Finkel, Richard S; Darras, Basil T; Muntoni, Francesco; Mercuri, Eugenio; De Vivo, Darryl C; Bishop, Kathie M; Schneider, Eugene; Bennett, C Frank; Foster, Richard; Farwell, Wildon.
Afiliação
  • Montes J; Department of Rehabilitation and Regenerative Medicine, Columbia University Irving Medical Center, New York, New York.
  • Dunaway Young S; Department of Neurology, Columbia University Irving Medical Center, New York, New York.
  • Mazzone ES; Department of Neurology, Stanford University School of Medicine, Palo Alto, California.
  • Pasternak A; Department of Paediatric Neurology, Catholic University, Rome, Italy.
  • Glanzman AM; Department of Neurology, Boston Children's Hospital, Boston, Massachusetts.
  • Finkel RS; Department of Physical Therapy, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania.
  • Darras BT; Division of Neurology, Department of Pediatrics, Nemours Children's Hospital, Orlando, Florida.
  • Muntoni F; Department of Neurology, Boston Children's Hospital, Boston, Massachusetts.
  • Mercuri E; Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health and NIHR Great Ormond Street Hospital Biomedical Research Centre, London, UK.
  • De Vivo DC; Department of Paediatric Neurology, Catholic University, Rome, Italy.
  • Bishop KM; Department of Neurology, Columbia University Irving Medical Center, New York, New York.
  • Schneider E; Department Pediatrics, Columbia University Irving Medical Center, New York, New York.
  • Bennett CF; Clinical Development and Antisense Research, Ionis Pharmaceuticals, Inc, Carlsbad, California.
  • Foster R; Clinical Development and Antisense Research, Ionis Pharmaceuticals, Inc, Carlsbad, California.
  • Farwell W; Clinical Development and Antisense Research, Ionis Pharmaceuticals, Inc, Carlsbad, California.
Muscle Nerve ; 60(4): 409-414, 2019 10.
Article em En | MEDLINE | ID: mdl-31298747

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Atrofia Muscular Espinal / Fadiga Tipo de estudo: Etiology_studies Limite: Adolescent / Child / Child, preschool / Female / Humans / Infant / Male Idioma: En Revista: Muscle Nerve Ano de publicação: 2019 Tipo de documento: Article País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Atrofia Muscular Espinal / Fadiga Tipo de estudo: Etiology_studies Limite: Adolescent / Child / Child, preschool / Female / Humans / Infant / Male Idioma: En Revista: Muscle Nerve Ano de publicação: 2019 Tipo de documento: Article País de publicação: Estados Unidos