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Small molecule targeting r(UGGAA)n disrupts RNA foci and alleviates disease phenotype in Drosophila model.
Shibata, Tomonori; Nagano, Konami; Ueyama, Morio; Ninomiya, Kensuke; Hirose, Tetsuro; Nagai, Yoshitaka; Ishikawa, Kinya; Kawai, Gota; Nakatani, Kazuhiko.
Afiliação
  • Shibata T; Department of Regulatory Bioorganic Chemistry, The Institute of Scientific and Industrial Research (ISIR), Osaka University, Ibaraki, Japan.
  • Nagano K; Department of Life and Environmental Sciences, Faculty of Engineering, Chiba Institute of Technology, Chiba, Japan.
  • Ueyama M; Department of Neurotherapeutics, Osaka University Graduate School of Medicine, Suita, Japan.
  • Ninomiya K; Graduate School of Frontier Biosciences, Osaka University, Suita, Japan.
  • Hirose T; Graduate School of Frontier Biosciences, Osaka University, Suita, Japan.
  • Nagai Y; Institute for Genetic Medicine, Hokkaido University, Sapporo, Japan.
  • Ishikawa K; Department of Neurotherapeutics, Osaka University Graduate School of Medicine, Suita, Japan.
  • Kawai G; Center for Personalized Medicine for Healthy Aging, Tokyo Medical and Dental University, Tokyo, Japan.
  • Nakatani K; Department of Life and Environmental Sciences, Faculty of Engineering, Chiba Institute of Technology, Chiba, Japan.
Nat Commun ; 12(1): 236, 2021 01 11.
Article em En | MEDLINE | ID: mdl-33431896

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: RNA / Drosophila Limite: Animals / Humans Idioma: En Revista: Nat Commun Assunto da revista: BIOLOGIA / CIENCIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Japão País de publicação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: RNA / Drosophila Limite: Animals / Humans Idioma: En Revista: Nat Commun Assunto da revista: BIOLOGIA / CIENCIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Japão País de publicação: Reino Unido