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Long-term safety of lumacaftor-ivacaftor in children aged 2-5 years with cystic fibrosis homozygous for the F508del-CFTR mutation: a multicentre, phase 3, open-label, extension study.
Hoppe, Jordana E; Chilvers, Mark; Ratjen, Felix; McNamara, John J; Owen, Caroline A; Tian, Simon; Zahigian, Rachel; Cornell, Alexandra G; McColley, Susanna A.
Afiliação
  • Hoppe JE; Department of Pediatrics, Children's Hospital Colorado, University of Colorado School of Medicine, Aurora, CO, USA. Electronic address: jordana.hoppe@childrenscolorado.org.
  • Chilvers M; Department of Pediatrics, British Columbia Children's Hospital, University of British Columbia, Vancouver, BC, Canada.
  • Ratjen F; Department of Pediatrics, Hospital for Sick Children, Toronto, ON, Canada.
  • McNamara JJ; Children's Respiratory and Critical Care Specialists, Minneapolis, MN, USA.
  • Owen CA; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • Tian S; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • Zahigian R; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • Cornell AG; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • McColley SA; Department of Pediatrics, Northwestern University Feinberg School of Medicine, Chicago, IL, USA; Stanley Manne Children's Research Institute, Chicago, IL, USA; Ann & Robert H Lurie Children's Hospital of Chicago, Chicago, IL, USA.
Lancet Respir Med ; 9(9): 977-988, 2021 09.
Article em En | MEDLINE | ID: mdl-33965000

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística Limite: Child / Child, preschool / Humans Idioma: En Revista: Lancet Respir Med Ano de publicação: 2021 Tipo de documento: Article País de publicação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística Limite: Child / Child, preschool / Humans Idioma: En Revista: Lancet Respir Med Ano de publicação: 2021 Tipo de documento: Article País de publicação: Reino Unido