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Genome Editing With TALEN, CRISPR-Cas9 and CRISPR-Cas12a in Combination With AAV6 Homology Donor Restores T Cell Function for XLP.
Houghton, Benjamin C; Panchal, Neelam; Haas, Simone A; Chmielewski, Kay O; Hildenbeutel, Markus; Whittaker, Thomas; Mussolino, Claudio; Cathomen, Toni; Thrasher, Adrian J; Booth, Claire.
Afiliação
  • Houghton BC; Molecular and Cellular Immunology, UCL Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Panchal N; Molecular and Cellular Immunology, UCL Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Haas SA; Institute for Transfusion Medicine and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany.
  • Chmielewski KO; Center for Chronic Immunodeficiency, Faculty of Medicine, University of Freiburg, Freiburg, Germany.
  • Hildenbeutel M; Institute for Transfusion Medicine and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany.
  • Whittaker T; Center for Chronic Immunodeficiency, Faculty of Medicine, University of Freiburg, Freiburg, Germany.
  • Mussolino C; Faculty of Biology, University of Freiburg, Freiburg, Germany.
  • Cathomen T; Institute for Transfusion Medicine and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany.
  • Thrasher AJ; Center for Chronic Immunodeficiency, Faculty of Medicine, University of Freiburg, Freiburg, Germany.
  • Booth C; Molecular and Cellular Immunology, UCL Great Ormond Street Institute of Child Health, London, United Kingdom.
Front Genome Ed ; 4: 828489, 2022.
Article em En | MEDLINE | ID: mdl-35677600

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Guideline Idioma: En Revista: Front Genome Ed Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Reino Unido País de publicação: Suíça

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Guideline Idioma: En Revista: Front Genome Ed Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Reino Unido País de publicação: Suíça