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MiR34 contributes to spinal muscular atrophy and AAV9-mediated delivery of MiR34a ameliorates the motor deficits in SMA mice.
Chen, Tai-Heng; Chang, Shih-Hsin; Wu, Yu-Fu; Yen, Ya-Ping; Hsu, Fang-Yu; Chen, Yen-Chung; Ming, Yang; Hsu, Ho-Chiang; Su, Yi-Ching; Wong, Sheng-Tang; Hung, Jui-Hung; Chiou, Shih-Hwa; Jong, Yuh-Jyh; Chen, Jun-An.
Afiliação
  • Chen TH; PhD Program in Translational Medicine, Kaohsiung Medical University, Kaohsiung 80708, and Academia Sinica, Taipei 11529, Taiwan.
  • Chang SH; Institute of Molecular Biology, Academia Sinica, Taipei 11529, Taiwan.
  • Wu YF; Department of Pediatrics, Kaohsiung Medical University, Kaohsiung 80708, Taiwan.
  • Yen YP; School of Post-Baccalaureate Medicine, Kaohsiung Medical University, Kaohsiung 80708, Taiwan.
  • Hsu FY; Institute of Molecular Biology, Academia Sinica, Taipei 11529, Taiwan.
  • Chen YC; Neuroscience Program of Academia Sinica, Academia Sinica, Taipei 11529, Taiwan.
  • Ming Y; Institute of Molecular Biology, Academia Sinica, Taipei 11529, Taiwan.
  • Hsu HC; Neuroscience Program of Academia Sinica, Academia Sinica, Taipei 11529, Taiwan.
  • Su YC; Institute of Molecular Biology, Academia Sinica, Taipei 11529, Taiwan.
  • Wong ST; Neuroscience Program of Academia Sinica, Academia Sinica, Taipei 11529, Taiwan.
  • Hung JH; Institute of Molecular Biology, Academia Sinica, Taipei 11529, Taiwan.
  • Chiou SH; Neuroscience Program of Academia Sinica, Academia Sinica, Taipei 11529, Taiwan.
  • Jong YJ; Institute of Molecular Biology, Academia Sinica, Taipei 11529, Taiwan.
  • Chen JA; Institute of Molecular Biology, Academia Sinica, Taipei 11529, Taiwan.
Mol Ther Nucleic Acids ; 32: 144-160, 2023 Jun 13.
Article em En | MEDLINE | ID: mdl-37064776

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Taiwan País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Taiwan País de publicação: Estados Unidos