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Apolipoprotein-mimetic nanodiscs reduce lipid accumulation and improve liver function in acid sphingomyelinase deficiency.
Halseth, Troy A; Correia, Adele B; Schultz, Mark L; Fawaz, Maria V; Kuiper, Esmée Q; Kumaran, Preethi; Dorsey, Kristen Hong; Schuchman, Edward H; Lieberman, Andrew P; Schwendeman, Anna.
Afiliação
  • Halseth TA; Department of Medicinal Chemistry, College of Pharmacy, University of Michigan, 428 Church St, Ann Arbor, MI 48109, USA.
  • Correia AB; Department of Pathology, University of Michigan Medical School, 3510 MSRB1, 1150 W. Medical Center Dr., Ann Arbor, MI, 48109, USA.
  • Schultz ML; Stead Family Department of Pediatrics, University of Iowa Carver College of Medicine, 2182 ML, Iowa City, IA 52242, USA.
  • Fawaz MV; Department of Medicinal Chemistry, College of Pharmacy, University of Michigan, 428 Church St, Ann Arbor, MI 48109, USA.
  • Kuiper EQ; Department of Pathology, University of Michigan Medical School, 3510 MSRB1, 1150 W. Medical Center Dr., Ann Arbor, MI, 48109, USA.
  • Kumaran P; Department of Pharmaceutical Sciences, College of Pharmacy, University of Michigan, 428 Church St, Ann Arbor, MI 48109, USA.
  • Dorsey KH; Department of Pharmaceutical Sciences, College of Pharmacy, University of Michigan, 428 Church St, Ann Arbor, MI 48109, USA.
  • Schuchman EH; Department of Genetics and Genomic Sciences, The Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.
  • Lieberman AP; Department of Pathology, University of Michigan Medical School, 3510 MSRB1, 1150 W. Medical Center Dr., Ann Arbor, MI, 48109, USA.
  • Schwendeman A; Department of Pharmaceutical Sciences, College of Pharmacy, University of Michigan, 428 Church St, Ann Arbor, MI 48109, USA; Biointerfaces Institute, NCRC, 2800 Plymouth Rd, Ann Arbor, MI 48109, USA. Electronic address: annaschw@umich.edu.
Nanomedicine ; 53: 102705, 2023 09.
Article em En | MEDLINE | ID: mdl-37633404

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Niemann-Pick Tipo A Limite: Animals / Humans Idioma: En Revista: Nanomedicine Assunto da revista: BIOTECNOLOGIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Niemann-Pick Tipo A Limite: Animals / Humans Idioma: En Revista: Nanomedicine Assunto da revista: BIOTECNOLOGIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos País de publicação: Estados Unidos