Detalhe da pesquisa
1.
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
N Engl J Med
; 384(21): 2002-2013, 2021 05 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-33974366
2.
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency.
Blood
; 138(15): 1304-1316, 2021 10 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-33974038
3.
Management of Late Twin-to-Twin Transfusion Syndrome beyond 26 Weeks: Comparison between Fetoscopic Laser Therapy versus Traditional Management.
Fetal Diagn Ther
; 50(6): 464-471, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37517395
4.
Fetal Laryngoscopy and Endoscopic Tracheal Intubation to Avoid ex utero Intrapartum Treatment in the Management of Fetuses with Suspected Airway Obstruction.
Fetal Diagn Ther
; 50(6): 472-479, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37544292
5.
Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patients.
Blood
; 129(19): 2624-2635, 2017 05 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-28351939
6.
Apheresis of Deceased Donors as a New Source of Mobilized Peripheral Blood Hematopoietic Stem Cells for Transplant Tolerance.
Transplantation
; 107(2): 504-510, 2023 02 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-35974436
7.
Evaluation of clonal hematopoiesis in pediatric ADA-SCID gene therapy participants.
Blood Adv
; 6(21): 5732-5736, 2022 11 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-35914227
8.
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency.
J Clin Invest
; 127(5): 1689-1699, 2017 May 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-28346229